ELEVATE, a Registry of Patients With Acute Hepatic Porphyria (AHP)

Last updated: February 13, 2026
Sponsor: Alnylam Pharmaceuticals
Overall Status: Active - Recruiting

Phase

N/A

Condition

N/A

Treatment

N/A

Clinical Study ID

NCT04883905
ALN-AS1-006
EUPAS43201
  • Ages > 12
  • All Genders

Study Summary

This global patient registry is being conducted to characterize the natural history and real-world clinical management of patients with AHP, and to further characterize the real-world safety and effectiveness of givosiran and other approved AHP therapies.

Eligibility Criteria

Inclusion

Inclusion Criteria:

  • Documented diagnosis of AHP, per physician's determination

Exclusion

Exclusion Criteria:

  • Currently enrolled in a clinical trial for any investigational agent

Study Design

Total Participants: 150
Study Start date:
April 26, 2021
Estimated Completion Date:
April 01, 2027

Connect with a study center

  • Clinical Trial Site

    Brussels 2800866,
    Belgium

    Active - Recruiting

  • Clinical Trial Site

    Leuven,
    Belgium

    Site Not Available

  • Clinical Trial Site

    Leuven 2792482,
    Belgium

    Active - Recruiting

  • Clinical Trial Site

    Bordeaux,
    France

    Site Not Available

  • Clinical Trial Site

    Bordeaux 3031582,
    France

    Active - Recruiting

  • Clinical Trial Site

    Paris,
    France

    Site Not Available

  • Clinical Trial Site

    Paris 2988507,
    France

    Active - Recruiting

  • Clinical Trial Site

    Toulouse,
    France

    Site Not Available

  • Clinical Trial Site

    Toulouse 2972315,
    France

    Active - Recruiting

  • Clinical Trial Site

    Berlin 2950159,
    Germany

    Active - Recruiting

  • Clinical Trial Site

    Chemnitz,
    Germany

    Site Not Available

  • Clinical Trial Site

    Chemnitz 2940132,
    Germany

    Active - Recruiting

  • Clinical Trial Site

    Münster,
    Germany

    Site Not Available

  • Clinical Trial Site

    Würzburg,
    Germany

    Site Not Available

  • Clinical Trial Site

    Würzburg 2805615,
    Germany

    Active - Recruiting

  • Clinical Trial Site

    Milan,
    Italy

    Site Not Available

  • Clinical Trial Site

    Milan 3173435,
    Italy

    Active - Recruiting

  • Clinical Trial Site

    Modena,
    Italy

    Site Not Available

  • Clinical Trial Site

    Modena 3173331,
    Italy

    Active - Recruiting

  • Clinical Trial Site

    Madrid 3117735,
    Spain

    Active - Recruiting

  • Clinical Trial Site

    Stockholm,
    Sweden

    Site Not Available

  • Clinical Trial Site

    Stockholm 2673730,
    Sweden

    Active - Recruiting

  • Clinical Trial Site

    Zurich 2657896,
    Switzerland

    Active - Recruiting

  • Clinical Trial Site

    Zürich,
    Switzerland

    Site Not Available

  • Clinical Trial Site

    Taichung,
    Taiwan

    Site Not Available

  • Clinical Trial Site

    Taichung 1668399,
    Taiwan

    Active - Recruiting

  • Clinical Trial Site

    Taipei,
    Taiwan

    Site Not Available

  • Clinical Trial Site

    Taipei 1668341,
    Taiwan

    Active - Recruiting

  • Clinical Trial Site

    Cardiff,
    United Kingdom

    Site Not Available

  • Clinical Trial Site

    Cardiff 2653822,
    United Kingdom

    Active - Recruiting

  • Clinical Trial Site

    London,
    United Kingdom

    Site Not Available

  • Clinical Trial Site

    London 2643743,
    United Kingdom

    Active - Recruiting

  • Clinical Trial Site

    Birmingham, Alabama 35233
    United States

    Site Not Available

  • Clinical Trial Site

    Birmingham 4049979, Alabama 4829764 35233
    United States

    Active - Recruiting

  • Clinical Trial Site

    Gilbert, Arizona 85234
    United States

    Site Not Available

  • Clinical Trial Site

    Gilbert 5295903, Arizona 5551752 85234
    United States

    Active - Recruiting

  • Clinical Trial Site

    San Francisco, California 90074
    United States

    Site Not Available

  • Clinical Trial Site

    San Francisco 5391959, California 5332921 90074
    United States

    Active - Recruiting

  • Clinical Trial Site

    Baltimore, Maryland 21205
    United States

    Site Not Available

  • Clinical Trial Site

    Baltimore 4347778, Maryland 4361885 21205
    United States

    Active - Recruiting

  • Clinical Trial Site

    Boston, Massachusetts 02114
    United States

    Site Not Available

  • Clinical Trial Site

    Boston 4930956, Massachusetts 6254926 02114
    United States

    Active - Recruiting

  • Clinical Trial Site

    Minneapolis, Minnesota 55455
    United States

    Site Not Available

  • Clinical Trial Site

    Minneapolis 5037649, Minnesota 5037779 55455
    United States

    Active - Recruiting

  • Clinical Trial Site

    New York, New York 10029
    United States

    Site Not Available

  • Clinical Trial Site

    New York 5128581, New York 5128638 10029
    United States

    Active - Recruiting

  • Clinical Trial Site

    Winston-Salem, North Carolina 27157
    United States

    Site Not Available

  • Clinical Trial Site

    Winston-Salem 4499612, North Carolina 4482348 27157
    United States

    Completed

  • Clinical Trial Site

    Oklahoma City, Oklahoma 73120
    United States

    Site Not Available

  • Clinical Trial Site

    Oklahoma City 4544349, Oklahoma 4544379 73120
    United States

    Active - Recruiting

  • Clinical Trial Site

    Philadelphia, Pennsylvania 19107
    United States

    Site Not Available

  • Clinical Trial Site

    Philadelphia 4560349, Pennsylvania 6254927 19107
    United States

    Completed

  • Clinical Trial Site

    Galveston, Texas 77555
    United States

    Site Not Available

  • Clinical Trial Site

    Galveston 4692883, Texas 4736286 77555
    United States

    Active - Recruiting

  • Clinical Trial Site

    Salt Lake City, Utah 84112
    United States

    Site Not Available

  • Clinical Trial Site

    Salt Lake City 5780993, Utah 5549030 84112
    United States

    Active - Recruiting

  • Clinical Trial Site

    Seattle, Washington 98195
    United States

    Site Not Available

  • Clinical Trial Site

    Seattle 5809844, Washington 5815135 98195
    United States

    Active - Recruiting

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