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Home » Drug Information » New Medical Therapies

Genetic Disease Trial Results

Click on a disease below to find trial results for all drug therapies in completed or ongoing clinical trials. Search results for other therapeutic areas or view all results for the current week.

  • Amyloidosis
  • Bipolar Disorder
  • Bronchiectasis
  • Celiac Disease
  • Cerebral Ischemia
  • Congenital Heart Disease
  • Congenital Lactic Acidosis (CLA)
  • Coronary Artery Disease
  • Cystic Fibrosis
  • Epilepsy
  • Epilepsy (Pediatric)
  • Fabry Disease
  • Familial Hypercholesterolemia
  • Gaucher Disease
  • Hemophilia
  • Hereditary Angioedema
  • Huntington's Disease
  • Iron Overload (Hemachromatosis)
  • Leber's Hereditary Optic Neuropathy (LHON)
  • Lysosomal Acid Lipase Deficiency (LAL)
  • Macular Degeneration
  • Phenylketonuria
  • Seizure Disorders
  • Sickle Cell Disease
  • Sjögren-Larsson Syndrome
  • Thalassemia
  • Wolman Disease

FDA Approvals

View the CenterWatch FDA Approved section for a listing of Genetic Disease

View

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