Genetic Disease Trial Results

Click on a disease below to find trial results for all drug therapies in completed or ongoing clinical trials. Search results for other therapeutic areas or view all results for the current week.

• Amyloidosis
• Bipolar Disorder
• Bronchiectasis
• Celiac Disease
• Cerebral Ischemia
• Congenital Heart Disease
• Congenital Lactic Acidosis (CLA)
• Coronary Artery Disease
• Cystic Fibrosis
• Epilepsy
• Epilepsy (Pediatric)
• Fabry Disease
• Familial Hypercholesterolemia
• Gaucher Disease
• Hemophilia
• Hereditary Angioedema
• Huntington's Disease
• Iron Overload (Hemachromatosis)
• Leber's Hereditary Optic Neuropathy (LHON)
• Lysosomal Acid Lipase Deficiency (LAL)
• Macular Degeneration
• Phenylketonuria
• Seizure Disorders
• Sickle Cell Disease
• Sjögren-Larsson Syndrome
• Thalassemia
• Wolman Disease