Phase
Condition
Pompe Disease
Liver Disorders
Treatment
N/AClinical Study ID
All Genders
Study Summary
Eligibility Criteria
Inclusion
Inclusion Criteria:
All patients with a confirmed diagnosis of Pompe disease who have signed the informed consent and authorization form(s) are eligible for inclusion. Confirmed diagnosis is defined as documented GAA enzyme deficiency from blood, skin, or muscle tissue and/or documentation of 2 GAA gene mutations.
Exclusion
Exclusion Criteria:
There are no exclusion criteria in this Registry
Study Design
Study Description
Connect with a study center
Investigational Site Number : 152218
Caba, Buenos Aires 1424
ArgentinaActive - Recruiting
Investigational Site Number : 153194
Caba, Buenos Aires CPC1181ACH
ArgentinaActive - Recruiting
Investigational Site Number :152218
Caba, Buenos Aires 1424
ArgentinaActive - Recruiting
Investigational Site Number :153194
Caba, Buenos Aires CPC1181ACH
ArgentinaActive - Recruiting
Investigational Site Number : 153032
Ciudad Autónoma de Buenos Aires, Buenos Aires 1425
ArgentinaActive - Recruiting
Investigational Site Number :153032
Ciudad Autónoma de Buenos Aires, Buenos Aires 1425
ArgentinaActive - Recruiting
Investigational Site Number :153032
Buenos Aires, 1425
ArgentinaSite Not Available
Investigational Site Number : 036013
Westmead, New South Wales 2145
AustraliaActive - Recruiting
Investigational Site Number : 151069
Westmead, New South Wales 2145
AustraliaActive - Recruiting
Investigational Site Number :036013
Westmead, New South Wales 2145
AustraliaActive - Recruiting
Investigational Site Number :151069
Westmead, New South Wales 2145
AustraliaActive - Recruiting
Investigational Site Number : 152096
Brisbane, Queensland 4101
AustraliaTerminated
Investigational Site Number : 154087
Brisbane, Queensland 4029
AustraliaActive - Recruiting
Investigational Site Number :152096
Brisbane, Queensland 4101
AustraliaSite Not Available
Investigational Site Number : 154087
Herston, Queensland 4006
AustraliaSite Not Available
Investigational Site Number :154087
Herston, Queensland 4006
AustraliaActive - Recruiting
Investigational Site Number : 151002
Adelaide, South Australia 5000
AustraliaActive - Recruiting
Investigational Site Number :151002
Adelaide, South Australia 5000
AustraliaActive - Recruiting
Investigational Site Number : 151015
Murdoch, Western Australia 6150
AustraliaActive - Recruiting
Investigational Site Number :151015
Murdoch, Western Australia 6150
AustraliaActive - Recruiting
Investigational Site Number : 150722
Antwerp, 2020
BelgiumActive - Recruiting
Investigational Site Number : 150722
Antwerpen, 2020
BelgiumSite Not Available
Investigational Site Number :150722
Antwerpen, 2020
BelgiumActive - Recruiting
Investigational Site Number : 154298
Bruges, 8000
BelgiumActive - Recruiting
Investigational Site Number : 154298
Brugge, 8000
BelgiumSite Not Available
Investigational Site Number :154298
Brugge, 8000
BelgiumActive - Recruiting
Investigational Site Number : 056010
Brussels, 1200
BelgiumActive - Recruiting
Investigational Site Number : 056010
Bruxelles, BE-1200
BelgiumActive - Recruiting
Investigational Site Number : 150684
Bruxelles, 1070
BelgiumActive - Recruiting
Investigational Site Number :056010
Bruxelles, BE-1200
BelgiumActive - Recruiting
Investigational Site Number :150684
Bruxelles, 1070
BelgiumActive - Recruiting
Investigational Site Number : 152072
Edegem, 2650
BelgiumActive - Recruiting
Investigational Site Number :152072
Edegem, 2650
BelgiumActive - Recruiting
Investigational Site Number : 152295
Gent, 9000
BelgiumActive - Recruiting
Investigational Site Number :152295
Gent, 9000
BelgiumActive - Recruiting
Investigational Site Number : 153179
Gosselies, 6041
BelgiumActive - Recruiting
Investigational Site Number :153179
Gosselies, 6041
BelgiumActive - Recruiting
Investigational Site Number : 151668
Leuven, 3000
BelgiumActive - Recruiting
Investigational Site Number : 152126
Leuven, 3000
BelgiumActive - Recruiting
Investigational Site Number :151668
Leuven, 3000
BelgiumActive - Recruiting
Investigational Site Number :152126
Leuven, 3000
BelgiumActive - Recruiting
Hospital Universitario Walter Cantidio - UFC Site Number : 076011
Fortaleza, Ceará 60430-370
BrazilActive - Recruiting
Hospital Universitario Walter Cantidio- Site Number : 076011
Fortaleza, Ceará 60430-270
BrazilActive - Recruiting
Investigational Site Number :076011
Fortaleza, Ceará 60430-370
BrazilActive - Recruiting
Hospital Geral e Maternidade de Cuiabá- Site Number : 076003
Cuiabá, Mato Grosso 78025-000
BrazilActive - Recruiting
Investigational Site Number :076003
Cuiabá, Mato Grosso 78025-000
BrazilSite Not Available
Hospital De Clinicas De Porto Alegre Site Number : 076008
Porto Alegre, Rio Grande Do Sul 90035-003
BrazilActive - Recruiting
Hospital de Clinicas de Porto Alegre- Site Number : 076008
Porto Alegre, Rio Grande Do Sul 90035-903
BrazilActive - Recruiting
Investigational Site Number :076008
Porto Alegre, Rio Grande Do Sul 90035-003
BrazilActive - Recruiting
Faculdade de Medicina de Ribeirao Preto - USP Site Number : 076009
Ribeirao Preto, São Paulo 14048-900
BrazilSite Not Available
Investigational Site Number :076009
Ribeirao Preto, São Paulo 14048-900
BrazilActive - Recruiting
Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto- Site Number : 076009
Ribeirão Preto, São Paulo 14049-900
BrazilActive - Recruiting
Investigational Site Number :076009
Ribeirão Preto, São Paulo 14048-900
BrazilSite Not Available
Instituto Fernandes Figueira - FIOCRUZ Site Number : 076001
Rio de Janeiro, 22250020
BrazilActive - Recruiting
Instituto Fernandes Figueira - FIOCRUZ- Site Number : 076001
Rio de Janeiro, 22250020
BrazilActive - Recruiting
Investigational Site Number :076001
Rio de Janeiro, 22250020
BrazilActive - Recruiting
Hospital das Clinicas FMUSP- Site Number : 076004
São Paulo, 05403-000
BrazilActive - Recruiting
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 076007
São Paulo, 05403-000
BrazilActive - Recruiting
Hospital das Clínicas da Faculdade de Medicina da USP Site Number : 076004
São Paulo, 05403-000
BrazilActive - Recruiting
Hospital das Clínicas da Faculdade de Medicina da USP Site Number : 076007
São Paulo, 05403-000
BrazilActive - Recruiting
Instituto de Genética e Erros Inatos do Metabolismo - IGEIM Site Number : 076002
São Paulo, 04020-041
BrazilActive - Recruiting
Instituto de Genética e Erros Inatos do Metabolismo - IGEIM- Site Number : 076002
São Paulo, 04020-041
BrazilActive - Recruiting
Investigational Site Number :076002
São Paulo, 04020-041
BrazilActive - Recruiting
Investigational Site Number :076004
São Paulo, 05403-000
BrazilActive - Recruiting
Investigational Site Number :076007
São Paulo, 05403-000
BrazilActive - Recruiting
Investigational Site Number :076012
São Paulo, 04037002
BrazilActive - Recruiting
Núcleo de Gestão em Pesquisa (NGP) - UNIFESP Site Number : 076012
São Paulo, 04037002
BrazilActive - Recruiting
Núcleo de Gestão em Pesquisa (NGP) - UNIFESP- Site Number : 076012
São Paulo, 04037002
BrazilActive - Recruiting
Investigational Site Number : 100001
Sofia, 1680
BulgariaActive - Recruiting
Investigational Site Number :100001
Sofia, 1680
BulgariaActive - Recruiting
Investigational Site Number : 124014
Calgary, Alberta T2M 0L6
CanadaActive - Recruiting
Investigational Site Number :124014
Calgary, Alberta T2M 0L6
CanadaSite Not Available
Investigational Site Number : 124002
Edmonton, Alberta TG62B7
CanadaActive - Recruiting
Investigational Site Number :124002
Edmonton, Alberta TG62B7
CanadaSite Not Available
Investigational Site Number : 124010
Vancouver, British Columbia V5Z1M9
CanadaActive - Recruiting
Investigational Site Number : 124011
Vancouver, British Columbia V6H3N1
CanadaActive - Recruiting
Investigational Site Number :124010
Vancouver, British Columbia V5Z1M9
CanadaActive - Recruiting
Investigational Site Number :124011
Vancouver, British Columbia V6H3N1
CanadaSite Not Available
Investigational Site Number : 124019
Winnipeg, Manitoba R3A1R9
CanadaActive - Recruiting
Investigational Site Number :124019
Winnipeg, Manitoba R3A1R9
CanadaSite Not Available
Investigational Site Number : 124022
Moncton, New Brunswick E1C 2Z3
CanadaActive - Recruiting
Investigational Site Number :124022
Moncton, New Brunswick E1C2Z3
CanadaActive - Recruiting
Investigational Site Number : 124007
Hamilton, Ontario L8N3Z5
CanadaActive - Recruiting
Investigational Site Number :124007
Hamilton, Ontario L8N3Z5
CanadaSite Not Available
Investigational Site Number : 124021
London, Ontario N6A 5W9
CanadaActive - Recruiting
Investigational Site Number :124021
London, Ontario N6A 5W9
CanadaActive - Recruiting
Investigational Site Number : 124006
Toronto, Ontario M5G 1X8
CanadaActive - Recruiting
Investigational Site Number :124006
Toronto, Ontario M5G 1X8
CanadaSite Not Available
Investigational Site Number : 124004
Montreal, Quebec H3A2B4
CanadaActive - Recruiting
Investigational Site Number : 124018
Montreal, Quebec H4A3J1
CanadaActive - Recruiting
Investigational Site Number :124004
Montreal, Quebec H3A2B4
CanadaActive - Recruiting
Investigational Site Number :124018
Montreal, Quebec H4A3J1
CanadaActive - Recruiting
Investigational Site Number : 124001
Sherbrooke, Quebec J1H5N4
CanadaActive - Recruiting
Investigational Site Number :124001
Sherbrooke, Quebec J1H5N4
CanadaSite Not Available
Investigational Site Number 124020
Halifax, B3K6R8
CanadaSite Not Available
Investigational Site Number : 152002
Punta Arenas,
ChileActive - Recruiting
Investigational Site Number :152002
Punta Arenas,
ChileActive - Recruiting
Investigational Site Number : 152001
Santiago,
ChileActive - Recruiting
Investigational Site Number :152001
Santiago,
ChileActive - Recruiting
Investigational Site Number : 152380
Beijing,
ChinaTerminated
Investigational Site Number : 153202
Beijing,
ChinaTerminated
Investigational Site Number : 153203
Beijing,
ChinaCompleted
Investigational Site Number :152380
Beijing,
ChinaTerminated
Investigational Site Number :153202
Beijing,
ChinaTerminated
Investigational Site Number :153203
Beijing,
ChinaCompleted
Investigational Site Number : 152379
Guangzhou, 510000
ChinaTerminated
Investigational Site Number :152379
Guangzhou, 510000
ChinaSite Not Available
Investigational Site Number : 152381
Jinan, 250014
ChinaTerminated
Investigational Site Number :152381
Jinan,
ChinaSite Not Available
Investigational Site Number : 152356
Shanghai, 200092
ChinaTerminated
Investigational Site Number : 152382
Shanghai,
ChinaTerminated
Investigational Site Number :152356
Shanghai, 200092
ChinaSite Not Available
Investigational Site Number :152382
Shanghai,
ChinaTerminated
Investigational Site Number : 170001
Bogota,
ColombiaActive - Recruiting
Investigational Site Number :170001
Bogota,
ColombiaActive - Recruiting
Investigational Site Number : 1910001
Zagreb, 10000
CroatiaActive - Recruiting
Investigational Site Number : 1910002
Zagreb, 10000
CroatiaActive - Recruiting
Investigational Site Number :1910001
Zagreb, 10000
CroatiaActive - Recruiting
Investigational Site Number :1910002
Zagreb, 10000
CroatiaActive - Recruiting
Investigational Site Number : 150809
Praha 2, 12808
CzechiaActive - Recruiting
Investigational Site Number :150809
Praha 2, 12808
CzechiaSite Not Available
Investigational Site Number :151229
København, 2100
DenmarkSite Not Available
Investigational Site Number : 151229
København Ø, 2100
DenmarkActive - Recruiting
Investigational Site Number :151229
København Ø, 2100
DenmarkActive - Recruiting
Investigational Site Number : 250003
BRON Cedex, 69677
FranceActive - Recruiting
Investigational Site Number : 250007
BRON Cedex, 69677
FranceActive - Recruiting
Investigational Site Number :250003
BRON Cedex, 69677
FranceActive - Recruiting
Investigational Site Number :250007
BRON Cedex, 69677
FranceActive - Recruiting
Investigational Site Number : 250010
Bordeaux, 33076
FranceActive - Recruiting
Investigational Site Number :250010
Bordeaux, 33000
FranceActive - Recruiting
Investigational Site Number : 250012
Brest, 29200
FranceActive - Recruiting
Investigational Site Number :250012
Brest, 29200
FranceActive - Recruiting
Investigational Site Number : 250009
Caen, 14033
FranceActive - Recruiting
Investigational Site Number :250009
Caen, 14000
FranceActive - Recruiting
Investigational Site Number : 250015
GRENOBLE cedex, 38043
FranceSite Not Available
Investigational Site Number :250015
GRENOBLE cedex, 38043
FranceActive - Recruiting
Investigational Site Number : 250015
La Tronche, 38700
FranceActive - Recruiting
Investigational Site Number : 250008
Lille, 59037
FranceActive - Recruiting
Investigational Site Number : 250008
Lille Cedex, 59037
FranceSite Not Available
Investigational Site Number :250008
Lille Cedex, 59037
FranceActive - Recruiting
Investigational Site Number : 250002
Marseille Cedex 05, 13385
FranceCompleted
Investigational Site Number :250002
Marseille Cedex 05, 13385
FranceCompleted
Investigational Site Number : 250017
NANCY Cedex, 54035
FranceSite Not Available
Investigational Site Number :250017
NANCY Cedex, 54035
FranceActive - Recruiting
Investigational Site Number : 250019
NANTES Cedex 1, 44035
FranceSite Not Available
Investigational Site Number :250019
NANTES Cedex 1, 44035
FranceActive - Recruiting
Investigational Site Number : 250011
NIMES Cedex 9, 30029
FranceSite Not Available
Investigational Site Number :250011
NIMES Cedex 9, 30029
FranceActive - Recruiting
Investigational Site Number : 250017
Nancy, 54035
FranceActive - Recruiting
Investigational Site Number : 250019
Nantes, 44093
FranceActive - Recruiting
Investigational Site Number : 250005
Nice Cedex 1, 06001
FranceActive - Recruiting
Investigational Site Number :250005
Nice cedex 1, 06001
FranceActive - Recruiting
Investigational Site Number : 250011
Nîmes, 30029
FranceActive - Recruiting
Investigational Site Number : 250001
PARIS Cedex 13, 75013
FranceSite Not Available
Investigational Site Number :250001
PARIS Cedex 13, 75013
FranceActive - Recruiting
Investigational Site Number : 250001
Paris, 75651
FranceActive - Recruiting
Investigational Site Number : 250004
Paris, 75015
FranceActive - Recruiting
Investigational Site Number :250004
Paris, 75015
FranceActive - Recruiting
Investigational Site Number : 250018
St Etienne, 42055
FranceSite Not Available
Investigational Site Number :250018
St Etienne, 42055
FranceActive - Recruiting
Investigational Site Number : 250018
St-priest-en-jarez, 42270
FranceActive - Recruiting
Investigational Site Number : 250016
Strasbourg, 67200
FranceActive - Recruiting
Investigational Site Number : 250016
Strasbourg Cedex 2, 67098
FranceSite Not Available
Investigational Site Number :250016
Strasbourg Cedex 2, 67098
FranceActive - Recruiting
Investigational Site Number : 250014
Toulouse, 31059
FranceActive - Recruiting
Investigational Site Number :250014
Toulouse, 31200
FranceActive - Recruiting
Investigational Site Number : 250006
Tours, 37032
FranceActive - Recruiting
Investigational Site Number :250006
Tours, 37044
FranceActive - Recruiting
Investigational Site Number :25013
Vannes, 56000
FranceSite Not Available
Investigational Site Number : 25013
Vannes Cedex, 56017
FranceActive - Recruiting
Investigational Site Number :25013
Vannes Cedex, 56017
FranceActive - Recruiting
Investigational Site Number : 151686
Berlin, 13353
GermanyActive - Recruiting
Investigational Site Number : 152041
Berlin, 13125
GermanyActive - Recruiting
Investigational Site Number : 152293
Berlin, 13353
GermanyActive - Recruiting
Investigational Site Number :151686
Berlin, 13353
GermanySite Not Available
Investigational Site Number :152041
Berlin, 13125
GermanyActive - Recruiting
Investigational Site Number :152293
Berlin, 13353
GermanyActive - Recruiting
Investigational Site Number : 152234
Bochum, 44789
GermanyActive - Recruiting
Investigational Site Number :152234
Bochum, 44789
GermanySite Not Available
Investigational Site Number : 152200
Bonn, 53127
GermanyActive - Recruiting
Investigational Site Number :152200
Bonn, 53105
GermanySite Not Available
Investigational Site Number : 152108
Freiburg, 79106
GermanyActive - Recruiting
Investigational Site Number :152108
Freiburg, 79106
GermanySite Not Available
Investigational Site Number : 154150
Gießen, 35392
GermanyActive - Recruiting
Investigational Site Number :154150
Gießen, 35392
GermanyActive - Recruiting
Investigational Site Number : 152045
Halle (Saale), 06120
GermanyActive - Recruiting
Investigational Site Number :152045
Halle (Saale), 06120
GermanySite Not Available
Investigational Site Number : 154215
Hamburg, 20354
GermanyActive - Recruiting
Investigational Site Number :154215
Hamburg, 20354
GermanyActive - Recruiting
Investigational Site Number : 150031
Mainz, 55131
GermanyActive - Recruiting
Investigational Site Number :150031
Mainz, 55131
GermanySite Not Available
Investigational Site Number : 152075
München, 80336
GermanyActive - Recruiting
Investigational Site Number :152075
München, 80336
GermanySite Not Available
Investigational Site Number : 152299
Münster, 48149
GermanyActive - Recruiting
Investigational Site Number :152299
Münster, 48149
GermanySite Not Available
Investigational Site Number : 300001
Thessaloniki, 546 42
GreeceActive - Recruiting
Investigational Site Number :300001
Thessaloniki, 54642
GreeceActive - Recruiting
Investigational Site Number 344001
Kowloon,
Hong KongSite Not Available
Investigational Site Number : 344001
Kowloon,
Hong KongActive - Recruiting
Investigational Site Number :344001
Kowloon,
Hong KongActive - Recruiting
Investigational Site Number : 3480009
Debrecen, 4032
HungaryActive - Recruiting
Investigational Site Number :3480009
Debrecen, 4032
HungaryActive - Recruiting
Investigational Site Number : 3480007
Nyíregyháza, 4400
HungaryActive - Recruiting
Investigational Site Number :3480007
Nyíregyháza, 4400
HungaryActive - Recruiting
Investigational Site Number : 3480011
Pã©cs, 7623
HungaryActive - Recruiting
Investigational Site Number : 3480011
Pécs, 7623
HungarySite Not Available
Investigational Site Number :3480011
Pécs, 7623
HungaryActive - Recruiting
Investigational Site Number : 3480012
Székesfehérvár, 8000
HungaryActive - Recruiting
Investigational Site Number :3480012
Székesfehérvár, 8000
HungaryActive - Recruiting
Investigational Site Number : 356003
Ahmedabad, 380015
IndiaActive - Recruiting
Investigational Site Number :356003
Ahmedabad, 380015
IndiaActive - Recruiting
Investigational Site Number : 356001
Kolkata, 700017
IndiaActive - Recruiting
Investigational Site Number :356001
Kolkata, 700017
IndiaActive - Recruiting
Investigational Site Number : 3560004
Secunderabad, 500026
IndiaActive - Recruiting
Investigational Site Number :3560004
Secunderabad, 500026
IndiaActive - Recruiting
Investigational Site Number : 356002
Vellore, 632004
IndiaActive - Recruiting
Investigational Site Number :356002
Vellore, 632004
IndiaActive - Recruiting
Investigational Site Number : 360001
Jakarta,
IndonesiaActive - Recruiting
Investigational Site Number :360001
Jakarta,
IndonesiaActive - Recruiting
Investigational Site Number : 3760002
Beer Sheva,
IsraelActive - Recruiting
Investigational Site Number :3760002
Beer Sheva,
IsraelSite Not Available
Investigational Site Number : 3760001
Haifa,
IsraelActive - Recruiting
Investigational Site Number :3760001
Haifa,
IsraelSite Not Available
Investigational Site Number : 3760003
Tel Aviv,
IsraelCompleted
Investigational Site Number :3760003
Tel Aviv,
IsraelCompleted
Investigational Site Number : 380008
Brescia, 25123
ItalyActive - Recruiting
Investigational Site Number :380008
Brescia, 25123
ItalyActive - Recruiting
Investigational Site Number : 380006
Cagliari, 09126
ItalyActive - Recruiting
Investigational Site Number :380006
Cagliari, 09126
ItalyActive - Recruiting
Investigational Site Number : 380014
Ferrara, 44124
ItalyActive - Recruiting
Investigational Site Number :380014
Ferrara, 44124
ItalyActive - Recruiting
Investigational Site Number : 380005
Firenze, 50141
ItalyActive - Recruiting
Investigational Site Number :380005
Firenze, 50141
ItalyActive - Recruiting
Investigational Site Number : 380004
Genova, 16147
ItalyActive - Recruiting
Investigational Site Number :380004
Genova, 16147
ItalyActive - Recruiting
Investigational Site Number : 380013
Messina, 98125
ItalyActive - Recruiting
Investigational Site Number :380013
Messina, 98125
ItalyActive - Recruiting
Investigational Site Number : 380007
Milan, 20133
ItalyActive - Recruiting
Investigational Site Number : 380007
Milano, 20133
ItalyActive - Recruiting
Investigational Site Number : 380016
Milano, 20122
ItalyActive - Recruiting
Investigational Site Number :380007
Milano, 20133
ItalyActive - Recruiting
Investigational Site Number :380016
Milano, 20122
ItalyActive - Recruiting
Investigational Site Number : 380009
Monza,
ItalyActive - Recruiting
Investigational Site Number :380009
Monza,
ItalyActive - Recruiting
Investigational Site Number : 380010
Napoli,
ItalyActive - Recruiting
Investigational Site Number : 380019
Napoli,
ItalyActive - Recruiting
Investigational Site Number :380010
Napoli,
ItalyActive - Recruiting
Investigational Site Number :380019
Napoli,
ItalyActive - Recruiting
Investigational Site Number : 380002
Padova, 35128
ItalyActive - Recruiting
Investigational Site Number : 380011
Padova,
ItalyActive - Recruiting
Investigational Site Number :380002
Padova, 35128
ItalyActive - Recruiting
Investigational Site Number :380011
Padova,
ItalyActive - Recruiting
Investigational Site Number : 380011
Padua, 35128
ItalyActive - Recruiting
Investigational Site Number : 380003
Pavia, 27100
ItalyActive - Recruiting
Investigational Site Number :380003
Pavia, 27100
ItalyActive - Recruiting
Investigational Site Number : 380012
Roma,
ItalyActive - Recruiting
Investigational Site Number : 380015
Roma, 00165
ItalyActive - Recruiting
Investigational Site Number :380012
Roma,
ItalyActive - Recruiting
Investigational Site Number :380015
Roma, 00165
ItalyActive - Recruiting
Investigational Site Number : 380017
Torino, 10126
ItalyActive - Recruiting
Investigational Site Number :380017
Torino, 10126
ItalyActive - Recruiting
Investigational Site Number : 380001
Udine, 33100
ItalyActive - Recruiting
Investigational Site Number :380001
Udine, 33100
ItalyActive - Recruiting
Investigational Site Number : 392106
Sakyo-ku, Kyoto 606-8507
JapanSite Not Available
Investigational Site Number :392106
Sakyo-ku, Kyoto 606-8507
JapanSite Not Available
Investigational Site Number : 392105
Ginowan, Okinawa 901-2214
JapanActive - Recruiting
Investigational Site Number :392105
Ginowan, Okinawa 901-2214
JapanActive - Recruiting
Investigational Site Number : 4000001
Amman, 261
JordanActive - Recruiting
Investigational Site Number :4000001
Amman, 261
JordanActive - Recruiting
Investigational Site Number : 151149
Seoul, Gyeonggi-do 05505
Korea, Republic ofActive - Recruiting
Investigational Site Number : 154148
Yangsan, Gyeongsangnam-do 50612
Korea, Republic ofActive - Recruiting
Investigational Site Number : 153178
Yangsan-si, Gyeongsangnam-do 50612
Korea, Republic ofActive - Recruiting
Investigational Site Number :153178
Yangsan-si, Gyeongsangnam-do 50612
Korea, Republic ofActive - Recruiting
Investigational Site Number : 153176
Seoul, Seoul-teukbyeolsi 06273
Korea, Republic ofActive - Recruiting
Investigational Site Number :153178
Busan,
Korea, Republic ofSite Not Available
Investigational Site Number : 153191
Daejeon,
Korea, Republic ofActive - Recruiting
Investigational Site Number :153191
Daejeon,
Korea, Republic ofActive - Recruiting
Investigational Site Number 153228
Jeju-si,
Korea, Republic ofSite Not Available
Investigational Site Number : 153225
Jeonnam,
Korea, Republic ofActive - Recruiting
Investigational Site Number :153225
Jeonnam,
Korea, Republic ofActive - Recruiting
Investigational Site Number : 153180
Seoul, 03080
Korea, Republic ofActive - Recruiting
Investigational Site Number : 153192
Seoul, 04401
Korea, Republic ofActive - Recruiting
Investigational Site Number : 153196
Seoul, 03080
Korea, Republic ofCompleted
Investigational Site Number : 153212
Seoul,
Korea, Republic ofActive - Recruiting
Investigational Site Number : 153222
Seoul,
Korea, Republic ofActive - Recruiting
Investigational Site Number :151149
Seoul, 05505
Korea, Republic ofActive - Recruiting
Investigational Site Number :153176
Seoul,
Korea, Republic ofActive - Recruiting
Investigational Site Number :153180
Seoul, 03080
Korea, Republic ofActive - Recruiting
Investigational Site Number :153192
Seoul, 04401
Korea, Republic ofActive - Recruiting
Investigational Site Number :153196
Seoul, 03080
Korea, Republic ofCompleted
Investigational Site Number :153212
Seoul,
Korea, Republic ofActive - Recruiting
Investigational Site Number :153222
Seoul,
Korea, Republic ofActive - Recruiting
Investigational Site Number :154148
Yangsan, 50612
Korea, Republic ofActive - Recruiting
Investigational Site Number : 154225
Kuwait,
KuwaitActive - Recruiting
Investigational Site Number :154225
Kuwait,
KuwaitActive - Recruiting
Investigational Site Number : 4220002
Beirut,
LebanonActive - Recruiting
Investigational Site Number : 4220004
Beirut, 11072210
LebanonActive - Recruiting
Investigational Site Number :4220004
Beirut, 11072210
LebanonActive - Recruiting
Investigational Site Number : 4220002
Hazmieh,
LebanonSite Not Available
Investigational Site Number :4220002
Hazmieh,
LebanonActive - Recruiting
Investigational Site Number : 458001
Jalan Pahang, 50586
MalaysiaActive - Recruiting
Investigational Site Number :458001
Jalan Pahang, 50586
MalaysiaActive - Recruiting
Investigational Site Number : 458002
Kuala Lumpur, 59100
MalaysiaActive - Recruiting
Investigational Site Number :458002
Kuala Lumpur, 59100
MalaysiaSite Not Available
Investigational Site Number : 458002
Lembah Pantai, 59100
MalaysiaSite Not Available
Investigational Site Number : 152029
Rotterdam, 3015 CE
NetherlandsActive - Recruiting
Investigational Site Number :152029
Rotterdam, 3015GD
NetherlandsActive - Recruiting
Investigational Site Number : 154264
Karachi,
PakistanActive - Recruiting
Investigational Site Number :154264
Karachi,
PakistanActive - Recruiting
Investigational Site Number : 154266
Lahore,
PakistanActive - Recruiting
Investigational Site Number :154266
Lahore,
PakistanActive - Recruiting
Investigational Site Number : 608001
Manila, 1000
PhilippinesActive - Recruiting
Investigational Site Number :608001
Manila, 1000
PhilippinesActive - Recruiting
Investigational Site Number : 150575
Warszawa, 04-730
PolandActive - Recruiting
Investigational Site Number :150575
Warszawa, 04-730
PolandActive - Recruiting
Investigational Site Number : 620008
Coimbra, 3000-075
PortugalActive - Recruiting
Investigational Site Number :620008
Coimbra, 3000-075
PortugalActive - Recruiting
Investigational Site Number : 620006
Lisboa, 1649-035
PortugalActive - Recruiting
Investigational Site Number :620006
Lisboa, 1649-035
PortugalActive - Recruiting
Investigational Site Number : 154099
Bucuresti, 022328
RomaniaActive - Recruiting
Investigational Site Number :154099
Bucuresti, 022328
RomaniaActive - Recruiting
Investigational Site Number : 643002
Moscow, 117218
Russian FederationCompleted
Investigational Site Number :643002
Moscow, 117218
Russian FederationCompleted
Investigational Site Number : 682004
Makkah, 21955
Saudi ArabiaActive - Recruiting
Investigational Site Number :682004
Makkah, 21955
Saudi ArabiaActive - Recruiting
Investigational Site Number : 682001
Qatif,
Saudi ArabiaActive - Recruiting
Investigational Site Number :682001
Qatif,
Saudi ArabiaActive - Recruiting
Investigational Site Number : 6880001
Belgrade, 11000
SerbiaActive - Recruiting
Investigational Site Number :6880001
Belgrade, 11000
SerbiaActive - Recruiting
Investigational Site Number : 702001
Singapore, 229899
SingaporeActive - Recruiting
Investigational Site Number :702001
Singapore, 229899
SingaporeActive - Recruiting
Investigational Site Number : 703001
Bratislava, 83340
SlovakiaActive - Recruiting
Investigational Site Number :703001
Bratislava, 83340
SlovakiaActive - Recruiting
Investigational Site Number : 154093
Chiayi,
TaiwanActive - Recruiting
Investigational Site Number :154093
Chiayi,
TaiwanActive - Recruiting
Investigational Site Number : 152152
Hualien,
TaiwanActive - Recruiting
Investigational Site Number :152152
Hualien,
TaiwanActive - Recruiting
Investigational Site Number : 152244
Kaohsiung, 807
TaiwanActive - Recruiting
Investigational Site Number :152244
Kaohsiung, 807
TaiwanActive - Recruiting
Investigational Site Number : 152246
Kaohsiung City, 833
TaiwanActive - Recruiting
Investigational Site Number : 152246
Kaohsiung Hsien,,
TaiwanSite Not Available
Investigational Site Number :152246
Kaohsiung Hsien,,
TaiwanActive - Recruiting
Investigational Site Number : 151534
New Taipei City, 23142
TaiwanActive - Recruiting
Investigational Site Number :151534
New Taipei City, 23142
TaiwanActive - Recruiting
Investigational Site Number : 151500
Putz City, Chia-yi,
TaiwanActive - Recruiting
Investigational Site Number :151500
Putz City, Chia-yi,
TaiwanActive - Recruiting
Investigational Site Number : 151179
Taichung, 404
TaiwanActive - Recruiting
Investigational Site Number : 151181
Taichung, 00407
TaiwanActive - Recruiting
Investigational Site Number :151181
Taichung, 00407
TaiwanActive - Recruiting
Investigational Site Number : 151179
Taichung City, 404
TaiwanSite Not Available
Investigational Site Number :151179
Taichung City, 404
TaiwanActive - Recruiting
Investigational Site Number : 152153
Tainan,
TaiwanActive - Recruiting
Investigational Site Number : 153248
Tainan, 70403
TaiwanSite Not Available
Investigational Site Number :152153
Tainan,
TaiwanActive - Recruiting
Investigational Site Number :153248
Tainan, 70403
TaiwanActive - Recruiting
Investigational Site Number : 152153
Tainan City, 710
TaiwanActive - Recruiting
Investigational Site Number : 153248
Tainan City, 704
TaiwanActive - Recruiting
Investigational Site Number : 151182
Taipei, 10041
TaiwanActive - Recruiting
Investigational Site Number : 152226
Taipei,
TaiwanActive - Recruiting
Investigational Site Number : 152321
Taipei, 10449
TaiwanActive - Recruiting
Investigational Site Number :151182
Taipei, 100
TaiwanActive - Recruiting
Investigational Site Number :152226
Taipei,
TaiwanActive - Recruiting
Investigational Site Number :152321
Taipei, 10449
TaiwanActive - Recruiting
Investigational Site Number : 151182
Taipei City, 100
TaiwanActive - Recruiting
Investigational Site Number : 152226
Taipei City, 112
TaiwanActive - Recruiting
Investigational Site Number : 153158
Tao Yuan County,
TaiwanSite Not Available
Investigational Site Number :153158
Tao Yuan County,
TaiwanActive - Recruiting
Investigational Site Number : 153158
Taoyuan City, 333
TaiwanActive - Recruiting
Investigational Site Number : 764001
Bangkok,
ThailandActive - Recruiting
Investigational Site Number : 764002
Bangkok, 10400
ThailandCompleted
Investigational Site Number : 764003
Bangkok, 10400
ThailandActive - Recruiting
Investigational Site Number : 764004
Bangkok, 10700
ThailandActive - Recruiting
Investigational Site Number :764001
Bangkok,
ThailandActive - Recruiting
Investigational Site Number :764002
Bangkok, 10400
ThailandCompleted
Investigational Site Number :764003
Bangkok, 10400
ThailandActive - Recruiting
Investigational Site Number :764004
Bangkok, 10700
ThailandActive - Recruiting
Investigational Site Number : 764005
Khon Kaen, 40002
ThailandActive - Recruiting
Investigational Site Number :764005
Khon Kaen, 40002
ThailandActive - Recruiting
Investigational Site Number :7840001
Dubai,
United Arab EmiratesSite Not Available
Investigational Site Number : 151340
Cambridge, Cambridgeshire CB2 2QQ
United KingdomActive - Recruiting
Investigational Site Number :151340
Cambridge, Cambridgeshire CB50QQ
United KingdomSite Not Available
Investigational Site Number : 152287
Birmingham, B15 2TH
United KingdomActive - Recruiting
Investigational Site Number : 154240
Birmingham, B46NH
United KingdomActive - Recruiting
Investigational Site Number :152287
Birmingham, B152TH
United KingdomActive - Recruiting
Investigational Site Number :154240
Birmingham, B46NH
United KingdomActive - Recruiting
Investigational Site Number : 152334
Cardiff, CF14 4XW
United KingdomActive - Recruiting
Investigational Site Number :152334
Cardiff, CF44XN
United KingdomSite Not Available
Investigational Site Number : 152156
Glasgow, G514TF
United KingdomActive - Recruiting
Investigational Site Number :152156
Glasgow, G514TF
United KingdomSite Not Available
Investigational Site Number : 150303
London, WC1N 3JH
United KingdomActive - Recruiting
Investigational Site Number : 151123
London, NW32QG
United KingdomActive - Recruiting
Investigational Site Number : 151646
London, NW1 2BU
United KingdomActive - Recruiting
Investigational Site Number :150303
London, WC1N3JH
United KingdomActive - Recruiting
Investigational Site Number :151123
London, NW32QG
United KingdomSite Not Available
Investigational Site Number :151646
London, WC1N3BG
United KingdomActive - Recruiting
Investigational Site Number : 150455
Manchester, M8 5RB
United KingdomActive - Recruiting
Investigational Site Number :150455
Manchester, M86RB
United KingdomSite Not Available
Investigational Site Number : 152087
Newcastle, NE13BZ
United KingdomActive - Recruiting
Investigational Site Number :152087
Newcastle, NE13BZ
United KingdomSite Not Available
Investigational Site Number : 150964
Salford, M6 8HD
United KingdomActive - Recruiting
Investigational Site Number :150964
Salford, M6 8HD
United KingdomSite Not Available
University Alabama at Birmingham Site Number : 840106
Birmingham, Alabama 35233
United StatesActive - Recruiting
University Alabama at Birmingham- Site Number : 840106
Birmingham, Alabama 35233
United StatesActive - Recruiting
University Alabama at Birmingham-Site Number:840106
Birmingham, Alabama 35233
United StatesActive - Recruiting
Barrow Neurological Institute- Site Number : 840087
Phoenix, Arizona 85013
United StatesActive - Recruiting
Barrow Neurological Institute-Site Number:840087
Phoenix, Arizona 85013
United StatesSite Not Available
Phoenix Children's Hospital- Site Number : 840003
Phoenix, Arizona 85013
United StatesActive - Recruiting
Phoenix Children's Hospital-Site Number:840003
Phoenix, Arizona 85013
United StatesActive - Recruiting
University of Arizona- Site Number : 840015
Tucson, Arizona 85724
United StatesActive - Recruiting
University of Arizona-Site Number:840015
Tucson, Arizona 85724
United StatesSite Not Available
Arkansas Childrens Hospital Site Number : 840109
Little Rock, Arkansas 72202
United StatesActive - Recruiting
Arkansas Childrens Hospital- Site Number : 840109
Little Rock, Arkansas 72202
United StatesActive - Recruiting
Arkansas Childrens Hospital-Site Number:840109
Little Rock, Arkansas 72202
United StatesActive - Recruiting
University of Arkansas for Medical Sciences Site Number : 840113
Little Rock, Arkansas 72205
United StatesActive - Recruiting
University of Arkansas for Medical Sciences- Site Number : 840113
Little Rock, Arkansas 72205
United StatesActive - Recruiting
University of Arkansas for Medical Sciences-Site Number:840113
Little Rock, Arkansas 72205
United StatesActive - Recruiting
University of California at Irvine- Site Number : 840036
Irvine, California 90211
United StatesActive - Recruiting
University of California at Irvine-Site Number:840036
Irvine, California 92697
United StatesSite Not Available
Loma Linda University- Genetics Site Number : 840070
Loma Linda, California 92354
United StatesCompleted
Loma Linda University- Genetics- Site Number : 840070
Loma Linda, California 92354
United StatesCompleted
Loma Linda University- Genetics-Site Number:840070
Loma Linda, California 92354
United StatesCompleted
Southern California Permanente Medical Group Site Number : 840108
Los Angeles, California 90027
United StatesActive - Recruiting
Southern California Permanente Medical Group- Site Number : 840108
Los Angeles, California 90027
United StatesActive - Recruiting
Southern California Permanente Medical Group-Site Number:840108
Los Angeles, California 90027
United StatesActive - Recruiting
USC Health Sciences Center Dept of Genetics- Site Number : 840082
Los Angeles, California 90033
United StatesActive - Recruiting
USC Health Sciences Center Dept of Genetics-Site Number:840082
Los Angeles, California 90033
United StatesActive - Recruiting
Children's Hospital Oakland Site Number : 840029
Oakland, California 94609
United StatesCompleted
Children's Hospital Oakland- Site Number : 840029
Oakland, California 94609
United StatesCompleted
Children's Hospital Oakland-Site Number:840029
Oakland, California 94609
United StatesCompleted
Children's Hospital of Orange County- Site Number : 840074
Orange, California 92868
United StatesActive - Recruiting
Children's Hospital of Orange County-Site Number:840074
Orange, California 92868
United StatesSite Not Available
UC Davis MIND Institute- Site Number : 840010
Sacramento, California 95817
United StatesActive - Recruiting
UC Davis MIND Institute-Site Number:840010
Sacramento, California 95817
United StatesSite Not Available
Loma Linda University Children's Hospital Site Number : 840117
San Bernardino, California 92408
United StatesActive - Recruiting
Loma Linda University Children's Hospital- Site Number : 840117
San Bernardino, California 92408
United StatesActive - Recruiting
Loma Linda University Children's Hospital-Site Number:840117
San Bernardino, California 92408
United StatesActive - Recruiting
University of California at San Diego Site Number : 840007
San Diego, California 92093
United StatesCompleted
University of California at San Diego- Site Number : 840007
San Diego, California 92093
United StatesCompleted
University of California at San Diego-Site Number:840007
San Diego, California 92093
United StatesCompleted
University of California at San Francisco- Site Number : 840051
San Francisco, California
United StatesActive - Recruiting
University of California at San Francisco-Site Number:840051
San Francisco, California
United StatesSite Not Available
Stanford University Pediatrics- Site Number : 840021
Stanford, California 94305
United StatesActive - Recruiting
Stanford University Pediatrics-Site Number:840021
Stanford, California 94305
United StatesSite Not Available
Children's Hospital IMD Clinic Site Number : 840069
Aurora, Colorado 80045
United StatesCompleted
Children's Hospital IMD Clinic- Site Number : 840069
Aurora, Colorado 80045
United StatesCompleted
Children's Hospital IMD Clinic-Site Number:840069
Aurora, Colorado 80045
United StatesCompleted
University of Colorado at Denver Genetics-Site Number:840068
Aurora, Colorado 80045
United StatesActive - Recruiting
Yale - Site Number : 840047
New Haven, Connecticut 06520
United StatesActive - Recruiting
Yale Site Number : 840047
New Haven, Connecticut 06520
United StatesActive - Recruiting
Yale-Site Number:840047
New Haven, Connecticut 06520
United StatesActive - Recruiting
Children's National Medical Center Site Number : 840067
Washington, District of Columbia 20010
United StatesActive - Recruiting
Children's National Medical Center- Site Number : 840067
Washington, District of Columbia 20010
United StatesActive - Recruiting
Children's National Medical Center-Site Number:840067
Washington, District of Columbia 20010
United StatesActive - Recruiting
University of Florida-Genetics Site Number : 840012
Gainesville, Florida 32610
United StatesActive - Recruiting
University of Florida-Genetics- Site Number : 840012
Gainesville, Florida 32610
United StatesActive - Recruiting
University of Florida-Genetics-Site Number:840012
Gainesville, Florida 32610
United StatesActive - Recruiting
The Atwal Clinic Site Number : 840112
Jacksonville, Florida 32216
United StatesActive - Recruiting
The Atwal Clinic- Site Number : 840112
Jacksonville, Florida 32216
United StatesActive - Recruiting
The Atwal Clinic-Site Number:840112
Jacksonville, Florida 32216
United StatesActive - Recruiting
University of Florida Pediatrics Genetics Site Number : 840121
Jacksonville, Florida 32207
United StatesActive - Recruiting
University of Florida Pediatrics Genetics- Site Number : 840121
Jacksonville, Florida 32207
United StatesActive - Recruiting
University of Florida Pediatrics Genetics-Site Number:840121
Jacksonville, Florida 32207
United StatesActive - Recruiting
University Of Miami SOM- Site Number : 840006
Miami, Florida 33136
United StatesActive - Recruiting
University Of Miami SOM-Site Number:840006
Miami, Florida 33136
United StatesSite Not Available
University of Florida-Genetics Site Number : 840096
Tampa, Florida 33606
United StatesActive - Recruiting
University of Florida-Genetics- Site Number : 840096
Tampa, Florida 33606
United StatesActive - Recruiting
University of Florida-Genetics-Site Number:840096
Tampa, Florida 33606
United StatesActive - Recruiting
Emory University School of Medicine- Human Genetics Site Number : 840060
Decatur, Georgia 30033
United StatesActive - Recruiting
Emory University School of Medicine- Human Genetics- Site Number : 840060
Decatur, Georgia 30033
United StatesActive - Recruiting
Emory University School of Medicine- Human Genetics-Site Number:840060
Decatur, Georgia 30033
United StatesActive - Recruiting
University of Colorado at Denver Genetics- Site Number : 840068
Aurora, Illinois 80045
United StatesActive - Recruiting
Ann and Robert Lurie Children's Hospital Site Number : 840011
Chicago, Illinois 60611
United StatesActive - Recruiting
Ann and Robert Lurie Children's Hospital Site Number : 840013
Chicago, Illinois 60611
United StatesActive - Recruiting
Ann and Robert Lurie Children's Hospital- Site Number : 840011
Chicago, Illinois 60611
United StatesActive - Recruiting
Ann and Robert Lurie Children's Hospital- Site Number : 840013
Chicago, Illinois 60611
United StatesActive - Recruiting
Ann and Robert Lurie Children's Hospital-Site Number:840011
Chicago, Illinois 60611
United StatesActive - Recruiting
Ann and Robert Lurie Children's Hospital-Site Number:840013
Chicago, Illinois 60611
United StatesActive - Recruiting
Rush University Medical Center Genetics Site Number : 840079
Chicago, Illinois 60612
United StatesActive - Recruiting
Rush University Medical Center Genetics- Site Number : 840079
Chicago, Illinois 60612
United StatesActive - Recruiting
Rush University Medical Center Genetics-Site Number:840079
Chicago, Illinois 60612
United StatesActive - Recruiting
Indianapolis University School of Medicine Site Number : 840027
Indianapolis, Indiana 46202
United StatesActive - Recruiting
Indianapolis University School of Medicine- Site Number : 840027
Indianapolis, Indiana 46202
United StatesActive - Recruiting
Indianapolis University School of Medicine-Site Number:840027
Indianapolis, Indiana 46202
United StatesActive - Recruiting
University of Iowa- Site Number : 840032
Iowa City, Iowa 52242
United StatesActive - Recruiting
University of Iowa-Site Number:840032
Iowa City, Iowa 52242
United StatesSite Not Available
University Of Kansas Medical Center Site Number : 840020
Kansas City, Kansas 66160
United StatesActive - Recruiting
University Of Kansas Medical Center-Site Number:840020
Kansas City, Kansas 66160
United StatesActive - Recruiting
University of Kansas Medical Center- Site Number : 840020
Kansas City, Kansas 66160
United StatesActive - Recruiting
University of Louisville- Genetics Site Number : 840030
Louisville, Kentucky 40202
United StatesActive - Recruiting
University of Louisville- Genetics- Site Number : 840030
Louisville, Kentucky 40202
United StatesActive - Recruiting
University of Louisville- Genetics-Site Number:840030
Louisville, Kentucky 40202
United StatesActive - Recruiting
Ochsner Medical Center - Site Number : 840120
New Orleans, Louisiana 70121
United StatesActive - Recruiting
Ochsner Medical Center Site Number : 840120
New Orleans, Louisiana 70121
United StatesActive - Recruiting
Ochsner Medical Center-Site Number:840120
New Orleans, Louisiana 70121
United StatesActive - Recruiting
Maine Medical Center Pediatrics Site Number : 840064
Portland, Maine 04102
United StatesActive - Recruiting
Maine Medical Center Pediatrics- Site Number : 840064
Portland, Maine 04102
United StatesActive - Recruiting
Maine Medical Center Pediatrics-Site Number:840064
Portland, Maine 04102
United StatesActive - Recruiting
John Hopkins Site Number : 840044
Baltimore, Maryland
United StatesActive - Recruiting
John Hopkins- Site Number : 840044
Baltimore, Maryland
United StatesActive - Recruiting
John Hopkins-Site Number:840044
Baltimore, Maryland
United StatesActive - Recruiting
Boston Children's Hospital Site Number : 840092
Boston, Massachusetts 2115
United StatesActive - Recruiting
Boston Children's Hospital- Site Number : 840092
Boston, Massachusetts 2115
United StatesActive - Recruiting
Boston Children's Hospital-Site Number:840092
Boston, Massachusetts 2115
United StatesActive - Recruiting
Massachusetts General Hospital-Genetics Site Number : 840062
Boston, Massachusetts 02114
United StatesActive - Recruiting
Massachusetts General Hospital-Genetics- Site Number : 840062
Boston, Massachusetts 02114
United StatesActive - Recruiting
Massachusetts General Hospital-Genetics-Site Number:840062
Boston, Massachusetts 02114
United StatesActive - Recruiting
Baystate Health Site Number : 840002
Springfield, Massachusetts 01199
United StatesActive - Recruiting
Baystate Health- Site Number : 840002
Springfield, Massachusetts 01199
United StatesActive - Recruiting
Baystate Health-Site Number:840002
Springfield, Massachusetts 01199
United StatesActive - Recruiting
University of Michigan Pediatrics Site Number : 840107
Ann Arbor, Michigan 48109
United StatesActive - Recruiting
University of Michigan Pediatrics- Site Number : 840107
Ann Arbor, Michigan 48109
United StatesActive - Recruiting
University of Michigan Pediatrics-Site Number:840107
Ann Arbor, Michigan 48109
United StatesActive - Recruiting
Children's Hospital of Michigan- Site Number : 840066
Detroit, Michigan 48201
United StatesActive - Recruiting
Children's Hospital of Michigan-Site Number:840066
Detroit, Michigan 48201
United StatesSite Not Available
Infusion Associates Site Number : 840050
Grand Rapids, Michigan 49525
United StatesActive - Recruiting
Infusion Associates- Site Number : 840050
Grand Rapids, Michigan 49525
United StatesActive - Recruiting
Infusion Associates-Site Number:840050
Grand Rapids, Michigan 49525
United StatesActive - Recruiting
Spectrum for Health Site Number : 840019
Grand Rapids, Michigan 49503
United StatesActive - Recruiting
Spectrum for Health- Site Number : 840019
Grand Rapids, Michigan 49503
United StatesActive - Recruiting
Spectrum for Health-Site Number:840019
Grand Rapids, Michigan 49503
United StatesActive - Recruiting
Children's Health Care Site Number : 840114
Minneapolis, Minnesota 55404
United StatesActive - Recruiting
Children's Health Care- Site Number : 840114
Minneapolis, Minnesota 55404
United StatesActive - Recruiting
Children's Health Care-Site Number:840114
Minneapolis, Minnesota 55404
United StatesActive - Recruiting
Children's Hospital and Clinics of Minnesota Site Number : 840046
Minneapolis, Minnesota 55404
United StatesCompleted
Children's Hospital and Clinics of Minnesota- Site Number : 840046
Minneapolis, Minnesota 55404
United StatesCompleted
Children's Hospital and Clinics of Minnesota-Site Number:840046
Minneapolis, Minnesota 55404
United StatesCompleted
University of Minnesota Medical Center Pediatrics- Site Number : 840035
Minneapolis, Minnesota 55455
United StatesActive - Recruiting
University of Minnesota Medical Center Pediatrics- Site Number : 840076
Minneapolis, Minnesota 55455
United StatesActive - Recruiting
University of Minnesota Medical Center Pediatrics-Site Number:840035
Minneapolis, Minnesota 55455
United StatesActive - Recruiting
University of Minnesota Medical Center Pediatrics-Site Number:840076
Minneapolis, Minnesota 55455
United StatesActive - Recruiting
University of Missouri Health System Department of Genetics Site Number : 840031
Columibia, Missouri 65212
United StatesActive - Recruiting
University of Missouri Health System Department of Genetics- Site Number : 840031
Columibia, Missouri 65212
United StatesActive - Recruiting
University of Missouri Health System Department of Genetics-Site Number:840031
Columibia, Missouri 65212
United StatesActive - Recruiting
Children's Mercy Hospital- Pediatrics Site Number : 840063
Kansas City, Missouri 64108
United StatesCompleted
Children's Mercy Hospital- Pediatrics- Site Number : 840063
Kansas City, Missouri 64108
United StatesCompleted
Children's Mercy Hospital- Pediatrics-Site Number:840063
Kansas City, Missouri 64108
United StatesCompleted
Washington University of St. Louis Site Number : 840100
Saint Louis, Missouri 63110
United StatesActive - Recruiting
Washington University of St. Louis- Site Number : 840100
Saint Louis, Missouri 63110
United StatesActive - Recruiting
Washington University of St. Louis-Site Number:840100
Saint Louis, Missouri 63110
United StatesActive - Recruiting
Investigational Site Number 840090
Helena, Montana 59601
United StatesSite Not Available
University of Nebraska Medical Center- Pediatrics Site Number : 840084
Omaha, Nebraska 68198
United StatesActive - Recruiting
University of Nebraska Medical Center- Pediatrics- Site Number : 840084
Omaha, Nebraska 68198
United StatesActive - Recruiting
University of Nebraska Medical Center- Pediatrics-Site Number:840084
Omaha, Nebraska 68198
United StatesActive - Recruiting
Children's Specialty Center of Nevada- Site Number : 840008
Las Vegas, Nevada 89109
United StatesActive - Recruiting
Children's Specialty Center of Nevada-Site Number:840008
Las Vegas, Nevada 89109
United StatesSite Not Available
Cooper Health Center- Site Number : 840098
Camden, New Jersey
United StatesTerminated
Cooper Health Center-Site Number:840098
Camden, New Jersey
United StatesSite Not Available
Hackensack University Medical Center Site Number : 840101
Hackensack, New Jersey 07601
United StatesActive - Recruiting
Hackensack University Medical Center- Site Number : 840101
Hackensack, New Jersey 07601
United StatesActive - Recruiting
Hackensack University Medical Center-Site Number:840101
Hackensack, New Jersey 07601
United StatesActive - Recruiting
Atlantic Health System Site Number : 840099
Morristown, New Jersey 07960
United StatesActive - Recruiting
Atlantic Health System- Site Number : 840099
Morristown, New Jersey 07962
United StatesActive - Recruiting
Atlantic Health System-Site Number:840099
Morristown, New Jersey 07960
United StatesActive - Recruiting
St. Peter's University Hospital Site Number : 840016
New Brunswick, New Jersey 08901
United StatesActive - Recruiting
St. Peter's University Hospital- Site Number : 840016
New Brunswick, New Jersey 08901
United StatesActive - Recruiting
St. Peter's University Hospital-Site Number:840016
New Brunswick, New Jersey 08901
United StatesActive - Recruiting
St. Joseph's Children's Hospital Site Number : 840057
Paterson, New Jersey 07503
United StatesActive - Recruiting
St. Joseph's Children's Hospital- Site Number : 840057
Paterson, New Jersey 07503
United StatesActive - Recruiting
St. Joseph's Children's Hospital-Site Number:840057
Paterson, New Jersey 07503
United StatesActive - Recruiting
Northwell Health Site Number : 840102
Manhasset, New York 11030
United StatesActive - Recruiting
Northwell Health- Site Number : 840102
Manhasset, New York 11030
United StatesActive - Recruiting
Northwell Health-Site Number:840102
Manhasset, New York 11030
United StatesActive - Recruiting
Metropolitan Hospital Center Site Number : 840110
New York, New York 10029-7494
United StatesActive - Recruiting
Metropolitan Hospital Center- Site Number : 840110
New York, New York 10029-7494
United StatesActive - Recruiting
Metropolitan Hospital Center-Site Number:840110
New York, New York 10029-7494
United StatesActive - Recruiting
Mt. Sinai School of Medicine Site Number : 840005
New York, New York 10029
United StatesActive - Recruiting
Mt. Sinai School of Medicine- Site Number : 840005
New York, New York 10029
United StatesActive - Recruiting
Mt. Sinai School of Medicine-Site Number:840005
New York, New York 10029
United StatesActive - Recruiting
New York University School Of Medicine Site Number : 840040
New York, New York 10016
United StatesActive - Recruiting
New York University School Of Medicine- Site Number : 840040
New York, New York 10016
United StatesActive - Recruiting
New York University School Of Medicine-Site Number:840040
New York, New York 10016
United StatesActive - Recruiting
University of Rochester Medical Center SOM Site Number : 840105
Rochester, New York 14642
United StatesActive - Recruiting
University of Rochester Medical Center SOM- Site Number : 840105
Rochester, New York 14642
United StatesActive - Recruiting
University of Rochester Medical Center SOM-Site Number:840105
Rochester, New York 14642
United StatesActive - Recruiting
State University of New York Site Number : 840052
Syracuse, New York 13210
United StatesActive - Recruiting
State University of New York- Site Number : 840052
Syracuse, New York 13210
United StatesActive - Recruiting
State University of New York-Site Number:840052
Syracuse, New York 13210
United StatesActive - Recruiting
New York Medical College Site Number : 840039
Valhalla, New York 10595
United StatesActive - Recruiting
New York Medical College- Site Number : 840039
Valhalla, New York 10595
United StatesActive - Recruiting
New York Medical College-Site Number:840039
Valhalla, New York 10595
United StatesActive - Recruiting
Carolinas Medical Center Hospital Site Number : 840065
Charlotte, North Carolina 28232
United StatesActive - Recruiting
Carolinas Medical Center Hospital- Site Number : 840065
Charlotte, North Carolina 28232
United StatesActive - Recruiting
Carolinas Medical Center Hospital-Site Number:840065
Charlotte, North Carolina 28232
United StatesActive - Recruiting
Duke University Medical Center Genetics Dept Site Number : 840037
Durham, North Carolina 27710
United StatesActive - Recruiting
Duke University Medical Center Genetics Dept- Site Number : 840037
Durham, North Carolina 27710
United StatesActive - Recruiting
Duke University Medical Center Genetics Dept-Site Number:840037
Durham, North Carolina 27710
United StatesActive - Recruiting
Cincinnati Children's Hospital-Genetics Site Number : 840041
Cincinnati, Ohio
United StatesActive - Recruiting
Cincinnati Children's Hospital-Genetics- Site Number : 840041
Cincinnati, Ohio
United StatesActive - Recruiting
Cincinnati Children's Hospital-Genetics-Site Number:840041
Cincinnati, Ohio
United StatesActive - Recruiting
Cleveland Clinic Foundation Pediatrics Site Number : 840048
Cleveland, Ohio 44195
United StatesActive - Recruiting
Cleveland Clinic Foundation Pediatrics- Site Number : 840048
Cleveland, Ohio 44195
United StatesActive - Recruiting
Cleveland Clinic Foundation Pediatrics-Site Number:840048
Cleveland, Ohio 44195
United StatesActive - Recruiting
UHCMC Site Number : 840119
Cleveland, Ohio 44106
United StatesActive - Recruiting
UHCMC- Site Number : 840119
Cleveland, Ohio 44106
United StatesActive - Recruiting
UHCMC-Site Number:840119
Cleveland, Ohio 44106
United StatesActive - Recruiting
Nationwide Children's Hospital Site Number : 840091
Columbus, Ohio 43205-2664
United StatesActive - Recruiting
Nationwide Children's Hospital- Site Number : 840091
Columbus, Ohio 43205-2664
United StatesActive - Recruiting
Nationwide Children's Hospital-Site Number:840091
Columbus, Ohio 43205-2664
United StatesActive - Recruiting
LSD Data Registry Site LLC Site Number : 840094
Dublin, Ohio 43017
United StatesActive - Recruiting
LSD Data Registry Site LLC- Site Number : 840094
Dublin, Ohio 43017
United StatesActive - Recruiting
LSD Data Registry Site LLC-Site Number:840094
Dublin, Ohio 43017
United StatesActive - Recruiting
Investigational Site Number 124002
Edmond, Oklahoma TG62B7
United StatesSite Not Available
Oregon Health & Science University-Site Number:840095
Portland, Oregon 97239
United StatesTerminated
Oregon Health & Sciences University Site Number : 840080
Portland, Oregon 97201
United StatesActive - Recruiting
Oregon Health & Sciences University- Site Number : 840080
Portland, Oregon 97201
United StatesActive - Recruiting
Oregon Health & Sciences University-Site Number:840080
Portland, Oregon 97201
United StatesActive - Recruiting
Oregon Health and Science University- Site Number : 840095
Portland, Oregon 97239
United StatesTerminated
Oregon Health and Scinece University- Site Number : 840038
Portland, Oregon 97239
United StatesTerminated
Oregon Health and Scinece University-Site Number:840038
Portland, Oregon 97239
United StatesTerminated
Penn Hershey Medical Center Site Number : 840061
Hershey, Pennsylvania 17033
United StatesActive - Recruiting
Penn Hershey Medical Center- Site Number : 840061
Hershey, Pennsylvania 17033
United StatesActive - Recruiting
Penn Hershey Medical Center-Site Number:840061
Hershey, Pennsylvania 17033
United StatesActive - Recruiting
Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089
Philadelphia, Pennsylvania 19104
United StatesActive - Recruiting
Children's Hospital of Philadelphia HUP Medical Genetics-Site Number:840089
Philadelphia, Pennsylvania 19104
United StatesActive - Recruiting
Children's Hospital of Philadelphia Site Number : 840034
Philadelphia, Pennsylvania
United StatesActive - Recruiting
Children's Hospital of Philadelphia- Site Number : 840034
Philadelphia, Pennsylvania
United StatesActive - Recruiting
Children's Hospital of Philadelphia-Site Number:840034
Philadelphia, Pennsylvania
United StatesActive - Recruiting
UPMC Site Number : 840014
Pittsburgh, Pennsylvania 15213
United StatesActive - Recruiting
UPMC- Site Number : 840014
Pittsburgh, Pennsylvania 15213
United StatesActive - Recruiting
UPMC-Site Number:840014
Pittsburgh, Pennsylvania 15213
United StatesActive - Recruiting
University of Pittsburgh Site Number : 840023
Pittsburgh, Pennsylvania 15224
United StatesActive - Recruiting
University of Pittsburgh- Site Number : 840023
Pittsburgh, Pennsylvania 15224
United StatesActive - Recruiting
University of Pittsburgh-Site Number:840023
Pittsburgh, Pennsylvania 15224
United StatesActive - Recruiting
Rhode Island Hospital Genetics Site Number : 840053
Providence, Rhode Island 02903
United StatesActive - Recruiting
Rhode Island Hospital Genetics- Site Number : 840053
Providence, Rhode Island 02903
United StatesActive - Recruiting
Rhode Island Hospital Genetics-Site Number:840053
Providence, Rhode Island 02903
United StatesActive - Recruiting
Greenwood Genetcs Site Number : 840055
Greenville, South Carolina 29605
United StatesActive - Recruiting
Greenwood Genetcs- Site Number : 840055
Greenville, South Carolina 29605
United StatesActive - Recruiting
Greenwood Genetcs-Site Number:840055
Greenville, South Carolina 29605
United StatesActive - Recruiting
Vanderbilt University Hospital-Pediatrics Site Number : 840049
Nashville, Tennessee 38232
United StatesActive - Recruiting
Vanderbilt University Hospital-Pediatrics- Site Number : 840049
Nashville, Tennessee 38232
United StatesActive - Recruiting
Vanderbilt University Hospital-Pediatrics-Site Number:840049
Nashville, Tennessee 38232
United StatesActive - Recruiting
Baylor Research Center Site Number : 840058
Dallas, Texas 75226
United StatesActive - Recruiting
Baylor Research Center- Site Number : 840058
Dallas, Texas 75226
United StatesActive - Recruiting
Baylor Research Center-Site Number:840058
Dallas, Texas 75226
United StatesActive - Recruiting
Cook Children's Health Care System Site Number : 840024
Fort Worth, Texas 76104
United StatesActive - Recruiting
Cook Children's Health Care System- Site Number : 840024
Fort Worth, Texas 76104
United StatesActive - Recruiting
Cook Children's Health Care System-Site Number:840024
Fort Worth, Texas 76104
United StatesActive - Recruiting
University of Utah Department of Medical Genetics- Site Number : 840043
Salt Lake City, Utah 84132
United StatesActive - Recruiting
University of Utah Department of Medical Genetics-Site Number:840043
Salt Lake City, Utah 84132
United StatesSite Not Available
University of Virginia School of Medicine-Pediatrics Site Number : 840078
Charlottesville, Virginia 22908
United StatesActive - Recruiting
University of Virginia School of Medicine-Pediatrics- Site Number : 840078
Charlottesville, Virginia 22908
United StatesActive - Recruiting
University of Virginia School of Medicine-Pediatrics-Site Number:840078
Charlottesville, Virginia 22908
United StatesActive - Recruiting
O&O Alpan, LLC Site Number : 840025
Fairfax, Virginia 22030
United StatesActive - Recruiting
O&O Alpan, LLC- Site Number : 840025
Fairfax, Virginia 22030
United StatesActive - Recruiting
O&O Alpan, LLC-Site Number:840025
Fairfax, Virginia 22030
United StatesActive - Recruiting
Children's Hospital of the Kings Daughters Site Number : 840072
Norfolk, Virginia 23507
United StatesActive - Recruiting
Children's Hospital of the Kings Daughters- Site Number : 840072
Norfolk, Virginia 23507
United StatesActive - Recruiting
Children's Hospital of the Kings Daughters-Site Number:840072
Norfolk, Virginia 23507
United StatesActive - Recruiting
Seattle Children's Hospital- Site Number : 840028
Seattle, Washington 98105
United StatesActive - Recruiting
Seattle Children's Hospital-Site Number:840028
Seattle, Washington 98105
United StatesSite Not Available
University Of Washington Medical Center- Site Number : 840059
Seattle, Washington 98195
United StatesActive - Recruiting
University Of Washington Medical Center-Site Number:840059
Seattle, Washington 98195
United StatesActive - Recruiting
Multicare Health System ¿ Mary Bridge Childrens Hospital Site Number : 840115
Tacoma, Washington 98415
United StatesActive - Recruiting
Multicare Health System ¿ Mary Bridge Childrens Hospital- Site Number : 840115
Tacoma, Washington 98415
United StatesActive - Recruiting
Multicare Health System ¿ Mary Bridge Childrens Hospital-Site Number:840115
Tacoma, Washington 98415
United StatesActive - Recruiting
Children's Hospital of Wisconsin-Pediatrics Site Number : 840054
Milwaukee, Wisconsin 53226
United StatesActive - Recruiting
Children's Hospital of Wisconsin-Pediatrics- Site Number : 840054
Milwaukee, Wisconsin 53226
United StatesActive - Recruiting
Children's Hospital of Wisconsin-Pediatrics-Site Number:840054
Milwaukee, Wisconsin 53226
United StatesActive - Recruiting
Investigational Site Number : 154212
Hanoi,
VietnamActive - Recruiting
Investigational Site Number :154212
Hanoi,
VietnamActive - Recruiting
Investigational Site Number : 704002
Ho Chi Minh City, 700000
VietnamActive - Recruiting
Investigational Site Number :704002
Ho Chi Minh City, 700000
VietnamActive - Recruiting
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