Phase
Condition
Cholesterol Ester Storage Disease (Cesd)
Wolman Disease
Treatment
N/AClinical Study ID
All Genders
Study Summary
Eligibility Criteria
Inclusion
Patients must have a confirmed diagnosis of LAL Deficiency. An Informed Consent and Authorization must be obtained prior to patient enrollment where required under applicable laws and regulations, or a waiver must be obtained by the Institutional Review Board/Independent Ethics Committee.
Patients cannot be currently participating in an Alexion-sponsored clinical trial. Patients who have concluded participation in an Alexion-sponsored sebelipase alfa clinical trial are eligible to enroll in this Registry, and enrollment in the Registry will not exclude a patient from enrolling in a future clinical trial.
Study Design
Study Description
Connect with a study center
Clinical Trial Site
New Lambton Heights, New South Wales 2305
AustraliaSite Not Available
Clinical Trial Site
New Lambton Heights 10103866, New South Wales 2155400 2305
AustraliaActive - Recruiting
New Lambton Heights,
AustraliaActive - Recruiting
Clinical Trial Site
Ghent, East Flanders 9000
BelgiumSite Not Available
Clinical Trial Site
Ghent 2797656, East Flanders 9000
BelgiumActive - Recruiting
Ghent,
BelgiumActive - Recruiting
empty
Woluwe-Saint-Lambert,
BelgiumSite Not Available
Clinical Trial Site
Campinas, São Paulo 13083-878
BrazilSite Not Available
Clinical Trial Site
Campinas 3467865, São Paulo 3448433 13083-878
BrazilActive - Recruiting
Campinas,
BrazilActive - Recruiting
empty
Ribeirão Preto,
BrazilSite Not Available
Clinical Trial Site
São Paulo, 04543-011
BrazilSite Not Available
São Paulo,
BrazilActive - Recruiting
Clinical Trial Site
São Paulo 3448439, 04543-011
BrazilActive - Recruiting
Clinical Trial Site
Sofia, Sofia City 1612
BulgariaSite Not Available
Clinical Trial Site
Sofia 727011, Sofia-Grad 731061 1612
BulgariaActive - Recruiting
Clinical Trial Site
Edmonton, Alberta T6G 2H7
CanadaSite Not Available
Clinical Trial Site
Edmonton 5946768, Alberta 5883102 T6G 2H7
CanadaActive - Recruiting
Clinical Trial Site
Halifax, Nova Scotia B3H 1V8
CanadaSite Not Available
Clinical Trial Site
Halifax 6324729, Nova Scotia 6091530 B3H 1V8
CanadaActive - Recruiting
Clinical Trial Site
London, Ontario NGA 5W9
CanadaActive - Recruiting
London, Ontario
CanadaActive - Recruiting
Clinical Trial Site
London 6058560, Ontario 6093943 NGA 5W9
CanadaActive - Recruiting
Edmonton,
CanadaActive - Recruiting
Halifax,
CanadaActive - Recruiting
Clinical Trial Site
Quebec, G1R 2J6
CanadaSite Not Available
Clinical Trial Site
Québec 6325494, G1R 2J6
CanadaActive - Recruiting
Clinical Trial Site
Zagreb, 10000
CroatiaSite Not Available
Zagreb,
CroatiaActive - Recruiting
Clinical Trial Site
Zagreb 3186886, 10000
CroatiaActive - Recruiting
Clinical Trial Site
Prague, Central Bohemia 3339576 128 00
CzechiaActive - Recruiting
Clinical Trial Site
Olomouc, 779 00
CzechiaSite Not Available
Olomouc,
CzechiaActive - Recruiting
Clinical Trial Site
Olomouc 3069011, 779 00
CzechiaActive - Recruiting
Prague,
CzechiaActive - Recruiting
empty
Copenhagen,
DenmarkSite Not Available
Clinical Trial Site
Bron, Auvergne-Rhône-Alpes 69500
FranceSite Not Available
Clinical Trial Site
Clermont-Ferrand, Auvergne-Rhône-Alpes 63003
FranceSite Not Available
Clinical Trial Site
Grenoble, Auvergne-Rhône-Alpes 38043
FranceSite Not Available
Clinical Trial Site
Bron 3029931, Auvergne-Rhône-Alpes 11071625 69500
FranceActive - Recruiting
Clinical Trial Site
Clermont-Ferrand 3024635, Auvergne-Rhône-Alpes 11071625 63003
FranceActive - Recruiting
Clinical Trial Site
Grenoble 3014728, Auvergne-Rhône-Alpes 11071625 38043
FranceActive - Recruiting
Clinical Trial Site
Caen, Normandy 14033
FranceSite Not Available
Clinical Trial Site
Caen 3029241, Normandy 11071621 14033
FranceActive - Recruiting
Clinical Trial Site
La Rochelle, Nouvelle-Aquitaine 17000
FranceSite Not Available
Clinical Trial Site
Niort, Nouvelle-Aquitaine 79021
FranceSite Not Available
Clinical Trial Site
La Rochelle 3006787, Nouvelle-Aquitaine 11071620 17000
FranceActive - Recruiting
Clinical Trial Site
Niort 2990355, Nouvelle-Aquitaine 11071620 79021
FranceActive - Recruiting
Clinical Trial Site
Nancy, Vandœuvre-lès-Nancy 54500
FranceSite Not Available
Clinical Trial Site
Nancy 2990999, Vandœuvre-lès-Nancy 54500
FranceActive - Recruiting
Clinical Trial Site
Paris, Île-de-France 75743
FranceSite Not Available
Clinical Trial Site
Paris 2988507, Île-de-France Region 3012874 75743
FranceActive - Recruiting
Bron,
FranceActive - Recruiting
Clermont-Ferrand,
FranceActive - Recruiting
Clinical Trial Site
Dijon, 21000
FranceSite Not Available
Clinical Trial Site
Dijon 3021372, 21000
FranceActive - Recruiting
empty
La Tronche,
FranceSite Not Available
empty
Lyon,
FranceSite Not Available
Nancy,
FranceActive - Recruiting
Clinical Trial Site
Nantes, 44093
FranceSite Not Available
Nantes,
FranceActive - Recruiting
Clinical Trial Site
Nantes 2990969, 44093
FranceActive - Recruiting
empty
Nice,
FranceSite Not Available
Paris,
FranceActive - Recruiting
Clinical Trial Site
Munich, Bavaria 81377
GermanySite Not Available
Clinical Trial Site
Munich 2867714, Bavaria 2951839 81377
GermanyActive - Recruiting
Clinical Trial Site
Essen, North Rhine-Westphalia 45122
GermanySite Not Available
Clinical Trial Site
Essen 2928810, North Rhine-Westphalia 2861876 45122
GermanyActive - Recruiting
Clinical Trial Site
Mainz, Rhineland-Palatinate 55131
GermanySite Not Available
Clinical Trial Site
Mainz 2874225, Rhineland-Palatinate 2847618 55131
GermanyActive - Recruiting
Clinical Trial Site
Berlin, 13353
GermanySite Not Available
Berlin,
GermanyActive - Recruiting
Clinical Trial Site
Berlin 2950159, 13353
GermanyActive - Recruiting
Essen,
GermanyActive - Recruiting
empty
Hochheim,
GermanySite Not Available
empty
Mainz, 55131
GermanySite Not Available
Munich,
GermanyActive - Recruiting
Clinical Trial Site
Athens, Attica 115 27
GreeceSite Not Available
Clinical Trial Site
Athens 264371, Attica 6692632 115 27
GreeceActive - Recruiting
Clinical Trial Site
Ioannina, Epirus 455 00
GreeceSite Not Available
Clinical Trial Site
Ioannina 261779, Epirus 6697804 455 00
GreeceActive - Recruiting
Clinical Trial Site
Thessaloniki, Macedonia 564 03
GreeceSite Not Available
Clinical Trial Site
Thessaloniki 734077, Macedonia 564 03
GreeceActive - Recruiting
Athens,
GreeceActive - Recruiting
Clinical Trial Site
Dublin, Leinster D01 XD99
IrelandSite Not Available
Clinical Trial Site
Dublin 2964574, Leinster 7521314 D01 XD99
IrelandActive - Recruiting
Dublin,
IrelandActive - Recruiting
Clinical Trial Site
Petah Tikva, Central 49202
IsraelSite Not Available
Clinical Trial Site
Petah Tikva 293918, Central District 294904 49202
IsraelActive - Recruiting
Clinical Trial Site
Haifa, 3436212
IsraelSite Not Available
Clinical Trial Site
Haifa 294801, 3436212
IsraelActive - Recruiting
Clinical Trial Site
Jerusalem, 9103102
IsraelSite Not Available
Jerusalem,
IsraelActive - Recruiting
Clinical Trial Site
Jerusalem 281184, 9103102
IsraelActive - Recruiting
Petah Tikva,
IsraelActive - Recruiting
Clinical Trial Site
Bari, Apulia 70126
ItalySite Not Available
Clinical Trial Site
Bari 3182351, Apulia 3169778 70126
ItalyActive - Recruiting
Clinical Trial Site
Napoli, Campania 80131
ItalySite Not Available
Clinical Trial Site
Napoli 9031661, Campania 3181042 80131
ItalyActive - Recruiting
Clinical Trial Site
Udine 3165072, Friuli Venezia Giulia 3176525 33100
ItalyActive - Recruiting
Clinical Trial Site
Udine, Friuli-Venezia Giulia 33100
ItalySite Not Available
Clinical Trial Site
Genova, Liguria 16147
ItalySite Not Available
Clinical Trial Site
Genoa 3176219, Liguria 3174725 16147
ItalyActive - Recruiting
Clinical Trial Site
Bergamo, Lombardy 24127
ItalySite Not Available
Clinical Trial Site
Milano, Lombardy 20122
ItalySite Not Available
Clinical Trial Site
Bergamo 3182164, Lombardy 3174618 24127
ItalyActive - Recruiting
Clinical Trial Site
Milan 3173435, Lombardy 3174618 20122
ItalyActive - Recruiting
Clinical Trial Site
Turin, Piedmont 10126
ItalySite Not Available
Clinical Trial Site
Turin 3165524, Piedmont 3170831 10126
ItalyActive - Recruiting
Clinical Trial Site
Florence, Tuscany 50139
ItalySite Not Available
Clinical Trial Site
Florence 3176959, Tuscany 3165361 50139
ItalyActive - Recruiting
Clinical Trial Site
Padova, Veneto 35128
ItalySite Not Available
Clinical Trial Site
Padua 3171728, Veneto 3164604 35128
ItalyActive - Recruiting
empty
Genoa,
ItalySite Not Available
Genova,
ItalyActive - Recruiting
Milano,
ItalyActive - Recruiting
empty
Torino, 10126
ItalySite Not Available
Turin,
ItalyActive - Recruiting
Clinical Trial Site
Zapopan, Jalisco 45116
MexicoSite Not Available
Clinical Trial Site
Zapopan 3979770, Jalisco 4004156 45116
MexicoActive - Recruiting
Clinical Trial Site
Aguascalientes, 20230
MexicoSite Not Available
Aguascalientes,
MexicoActive - Recruiting
Clinical Trial Site
Aguascalientes 4019233, 20230
MexicoActive - Recruiting
Clinical Trial Site
Mexico City, 06720
MexicoSite Not Available
Mexico City,
MexicoActive - Recruiting
Clinical Trial Site
Mexico City 3530597, 06720
MexicoActive - Recruiting
Zapopan,
MexicoActive - Recruiting
Clinical Trial Site
Amsterdam, North Holland 1105
NetherlandsSite Not Available
Clinical Trial Site
Amsterdam 2759794, North Holland 2749879 1105
NetherlandsActive - Recruiting
Amsterdam,
NetherlandsActive - Recruiting
empty
Warsaw,
PolandSite Not Available
Clinical Trial Site
Guimarães, Braga 4835
PortugalSite Not Available
Clinical Trial Site
Guimarães 2738752, Braga District 2742031 4835
PortugalActive - Recruiting
Guimarães,
PortugalActive - Recruiting
Clinical Trial Site
Lisbon, 1649
PortugalSite Not Available
Lisbon,
PortugalActive - Recruiting
Clinical Trial Site
Lisbon 2267057, 1649
PortugalActive - Recruiting
Clinical Trial Site
Petersburg, Leningradskaya Oblast' 536199 194100
RussiaActive - Recruiting
Clinical Trial Site
Moscow, Moscow Oblast 524925 119192
RussiaActive - Recruiting
Clinical Trial Site
Nizhny Novgorod 520555, Nizhny Novgorod Oblast 559838 603950
RussiaActive - Recruiting
Clinical Trial Site
Petersburg, Leningrad Oblast 194100
Russian FederationActive - Recruiting
Clinical Trial Site
Moscow, Moscow Oblast 119296
Russian FederationActive - Recruiting
Clinical Trial Site
Nizhny Novgorod, Nizhny Novgorod Oblast 603950
Russian FederationSite Not Available
empty
Jeddah,
Saudi ArabiaSite Not Available
Clinical Trial Site
Riyadh, 11426
Saudi ArabiaSite Not Available
Riyadh,
Saudi ArabiaActive - Recruiting
Clinical Trial Site
Riyadh 108410, 11426
Saudi ArabiaActive - Recruiting
Clinical Trial Site
Ljubljana, 1111
SloveniaSite Not Available
Ljubljana,
SloveniaActive - Recruiting
Clinical Trial Site
Ljubljana 3196359, 1111
SloveniaActive - Recruiting
Clinical Trial Site
Santiago de Compostela, A Coruña 15706
SpainSite Not Available
Clinical Trial Site
Santiago de Compostela 3109642, A Coruña 15706
SpainActive - Recruiting
Clinical Trial Site
Oviedo, Asturias 33011
SpainSite Not Available
Clinical Trial Site
Barakaldo, Biscay 48903
SpainSite Not Available
Clinical Trial Site
Barakaldo 3109453, Biscay 48903
SpainActive - Recruiting
Clinical Trial Site
Logroño, La Rioja 26006
SpainSite Not Available
Clinical Trial Site
Logroño 3118150, La Rioja 3336897 26006
SpainActive - Recruiting
Clinical Trial Site
Burela, Lugo 27880
SpainSite Not Available
Clinical Trial Site
Burela de Cabo 3127476, Lugo 27880
SpainActive - Recruiting
Clinical Trial Site
Malaga, Málaga 29010
SpainSite Not Available
Clinical Trial Site
Málaga 2514256, Málaga 29010
SpainActive - Recruiting
Clinical Trial Site
Oviedo 3114711, Principality of Asturias 3114710 33011
SpainActive - Recruiting
Clinical Trial Site
Reus, Tarragona 43204
SpainSite Not Available
Clinical Trial Site
Reus 3111933, Tarragona 43204
SpainActive - Recruiting
Clinical Trial Site
A Coruña, 15006
SpainSite Not Available
Clinical Trial Site
A Coruña 3119841, 15006
SpainActive - Recruiting
Clinical Trial Site
Albacete, 02006
SpainSite Not Available
Albacete,
SpainActive - Recruiting
Clinical Trial Site
Albacete 2522258, 02006
SpainActive - Recruiting
Clinical Trial Site
Alicante, 03203
SpainSite Not Available
Clinical Trial Site
Alicante 2521978, 03203
SpainActive - Recruiting
Hospital Regional Universitario de Málaga
Andalusia,
SpainSite Not Available
Hospital Universitario Miguel Servet
Aragon,
SpainSite Not Available
Hospital Universitario Central de Asturias
Asturias,
SpainSite Not Available
Clinical Trial Site
Barcelona, 08036
SpainSite Not Available
Barcelona,
SpainActive - Recruiting
Clinical Trial Site
Barcelona 3128760, 08305
SpainActive - Recruiting
Hospital Universitario de Cruces
Basque Country,
SpainSite Not Available
Hospital Universitario de Gran Canaria Dr. Negrín
Canary Islands,
SpainSite Not Available
Hospital Universitario Rio Hortega
Castile And León,
SpainSite Not Available
Complejo Hospitalario Universitario de Albacete
Castile-La Mancha,
SpainSite Not Available
Hospital Clinic i Provincial
Catalonia,
SpainActive - Recruiting
Hospital Universitario San Joan de Reus
Catalonia,
SpainActive - Recruiting
Hospital Universitario Valle Hebron
Catalonia,
SpainSite Not Available
Complejo Hospitalario Universitario de A Coruña - Hospital Teresa Herrera
Galicia,
SpainSite Not Available
Hospital Clínico Universitario Santiago de Compostela
Galicia,
SpainActive - Recruiting
Hospital Da Costa Burela
Galicia,
SpainActive - Recruiting
Hospital de San Pedro
La Rioja,
SpainSite Not Available
Clinical Trial Site
Las Palmas, 35019
SpainSite Not Available
Clinical Trial Site
Las Palmas 2515272, 35019
SpainActive - Recruiting
Clinical Trial Site
Madrid, 28914
SpainSite Not Available
Madrid,
SpainActive - Recruiting
Clinical Trial Site
Madrid 3117735, 28046
SpainActive - Recruiting
Clinical Trial Site
Murcia, 30120
SpainSite Not Available
Hospital Clínico Universitario Virgen de la Arrixaca
Murcia,
SpainActive - Recruiting
Clinical Trial Site
Murcia 2513416, 30120
SpainActive - Recruiting
Oviedo,
SpainActive - Recruiting
Hospital Universitario de Elche
Valencia,
SpainSite Not Available
Clinical Trial Site
Valladolid, 47012
SpainSite Not Available
Valladolid,
SpainActive - Recruiting
Clinical Trial Site
Valladolid 3106672, 47012
SpainActive - Recruiting
Clinical Trial Site
Zaragoza, 50009
SpainSite Not Available
Zaragoza,
SpainActive - Recruiting
Clinical Trial Site
Zaragoza 3104324, 50009
SpainActive - Recruiting
empty
Zürich,
SwitzerlandSite Not Available
Clinical Trial Site
Cambridge, Cambridgeshire CB2 0QQ
United KingdomSite Not Available
Clinical Trial Site
Cambridge 2653941, Cambridgeshire CB2 0QQ
United KingdomActive - Recruiting
Clinical Trial Site
London, Greater London WC1N 3BG
United KingdomSite Not Available
Clinical Trial Site
London 2643743, Greater London WC1N 3BG
United KingdomActive - Recruiting
Clinical Trial Site
Manchester, Greater Manchester M13 9WL
United KingdomSite Not Available
Clinical Trial Site
Manchester 2643123, Greater Manchester M13 9WL
United KingdomActive - Recruiting
Clinical Trial Site
Salford, Greater Manchester M6 8HD
United KingdomSite Not Available
Clinical Trial Site
Salford 2638671, Greater Manchester M6 8HD
United KingdomActive - Recruiting
Clinical Trial Site
Birmingham, West Midlands B4 6NH
United KingdomSite Not Available
Clinical Trial Site
Birmingham 2655603, West Midlands B4 6NH
United KingdomActive - Recruiting
Birmingham,
United KingdomActive - Recruiting
Cambridge,
United KingdomActive - Recruiting
empty
Greater Manchester,
United KingdomSite Not Available
London,
United KingdomActive - Recruiting
Manchester,
United KingdomActive - Recruiting
Salford,
United KingdomActive - Recruiting
Clinical Trial Site
Phoenix, Arizona 85016
United StatesSite Not Available
Phoenix, Arizona
United StatesActive - Recruiting
Clinical Trial Site
Phoenix 5308655, Arizona 5551752 85016
United StatesActive - Recruiting
empty
Los Angeles, California
United StatesSite Not Available
Clinical Trial Site
Stanford, California 94305
United StatesSite Not Available
Stanford, California 94305
United StatesActive - Recruiting
Clinical Trial Site
Stanford 5398563, California 5332921 94305
United StatesActive - Recruiting
Clinical Trial Site
Miramar, Florida 33025
United StatesSite Not Available
Clinical Trial Site
Orlando, Florida 32806
United StatesSite Not Available
Orlando, Florida
United StatesActive - Recruiting
Clinical Trial Site
Miramar 4164601, Florida 4155751 33025
United StatesActive - Recruiting
Clinical Trial Site
Orlando 4167147, Florida 4155751 32806
United StatesActive - Recruiting
Clinical Trial Site
Atlanta, Georgia 30322
United StatesSite Not Available
Atlanta, Georgia
United StatesActive - Recruiting
empty
Decatur, Georgia 30033
United StatesSite Not Available
Clinical Trial Site
Atlanta 4180439, Georgia 4197000 30322
United StatesActive - Recruiting
Clinical Trial Site
Chicago, Illinois 60611
United StatesSite Not Available
Chicago, Illinois 60611
United StatesActive - Recruiting
Clinical Trial Site
Chicago 4887398, Illinois 4896861 60611
United StatesActive - Recruiting
Clinical Trial Site
Boston, Massachusetts 02115
United StatesSite Not Available
Boston, Massachusetts 02115
United StatesActive - Recruiting
empty
Lexington, Massachusetts 02421
United StatesSite Not Available
Clinical Trial Site
Boston 4930956, Massachusetts 6254926 02115
United StatesActive - Recruiting
Clinical Trial Site
Detroit, Michigan 48236
United StatesSite Not Available
Detroit, Michigan 48236
United StatesActive - Recruiting
Clinical Trial Site
Detroit 4990729, Michigan 5001836 48236
United StatesActive - Recruiting
Clinical Trial Site
Minneapolis, Minnesota 55404
United StatesSite Not Available
Minneapolis, Minnesota 55111
United StatesActive - Recruiting
Clinical Trial Site
Minneapolis 5037649, Minnesota 5037779 55404
United StatesActive - Recruiting
Clinical Trial Site
Jackson, Mississippi 39216
United StatesSite Not Available
Clinical Trial Site
Jackson 4431410, Mississippi 4436296 39216
United StatesActive - Recruiting
empty
Hackensack, New Jersey
United StatesSite Not Available
Clinical Trial Site
Hackensack, NJ, 7601, New Jersey 07601
United StatesSite Not Available
Clinical Trial Site
Hackensack, NJ, 7601 5098706, New Jersey 5101760 07601
United StatesActive - Recruiting
Clinical Trial Site
Bronx, New York 10467
United StatesSite Not Available
Bronx, New York 10467
United StatesTerminated
Clinical Trial Site
New York, New York 10016
United StatesSite Not Available
New York, New York 11030
United StatesActive - Recruiting
empty
The Bronx, New York 10467
United StatesSite Not Available
Clinical Trial Site
New York 5128581, New York 5128638 10016
United StatesActive - Recruiting
Clinical Trial Site
The Bronx 5110266, New York 5128638 10467
United StatesActive - Recruiting
Clinical Trial Site
Philadelphia, Pennsylvania 19107
United StatesSite Not Available
Philadelphia, Pennsylvania
United StatesActive - Recruiting
Clinical Trial Site
Philadelphia 4560349, Pennsylvania 6254927 19104-6061
United StatesActive - Recruiting
empty
Providence, Rhode Island 02903
United StatesSite Not Available
empty
Dallas, Texas
United StatesSite Not Available
Clinical Trial Site
Houston, Texas 77030
United StatesSite Not Available
Houston, Texas 77030
United StatesActive - Recruiting
Clinical Trial Site
Snyder, Texas 79549
United StatesSite Not Available
Clinical Trial Site
Houston 4699066, Texas 4736286 77030
United StatesActive - Recruiting
Clinical Trial Site
Snyder 5530921, Texas 4736286 79549
United StatesActive - Recruiting
empty
Fairfax, Virginia 22030
United StatesSite Not Available
Clinical Trial Site
Tacoma, Washington 98405
United StatesSite Not Available
Tacoma, Washington
United StatesActive - Recruiting
Clinical Trial Site
Tacoma 5812944, Washington 5815135 98405
United StatesActive - Recruiting

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