ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

Last updated: February 11, 2025
Sponsor: Alnylam Pharmaceuticals
Overall Status: Active - Recruiting

Phase

N/A

Condition

Amyloidosis

Treatment

N/A

Clinical Study ID

NCT04561518
ALN-TTR02-013
  • All Genders

Study Summary

The purpose of this study is to:

  • Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosis patients

  • Characterize the safety and effectiveness of patisiran and vutrisiran as part of routine clinical practice in the real-world clinical setting

  • Describe disease emergence/progression in pre-symptomatic carriers of a known disease-causing transthyretin (TTR) variant

Eligibility Criteria

Inclusion

Inclusion Criteria:

  • Diagnosis of ATTR amyloidosis or documented known disease-causing TTR variant forthe cohort of pre-symptomatic carriers

  • Germany Only: Patients must be treated per the summary of product characteristics (SmPC) for any approved treatment for ATTR amyloidosis

Exclusion

Exclusion Criteria:

  • Current enrollment in a clinical trial for any investigational agent

Study Design

Total Participants: 1500
Study Start date:
November 23, 2020
Estimated Completion Date:
September 01, 2030

Connect with a study center

  • Clinical Trial Site

    Salvador,
    Brazil

    Active - Recruiting

  • Clinical Trial Site

    Sao Paulo,
    Brazil

    Active - Recruiting

  • Clinical Trial Site

    Sofia,
    Bulgaria

    Active - Recruiting

  • Clinical Trial Site

    Arhus,
    Denmark

    Active - Recruiting

  • Clinical Trial Site

    Copenhagen,
    Denmark

    Active - Recruiting

  • Clinical Trial Site

    Bordeaux,
    France

    Active - Recruiting

  • Clinical Trial Site

    Bron,
    France

    Active - Recruiting

  • Clinical Trial Site

    Créteil,
    France

    Active - Recruiting

  • Clinical Trial Site

    Le Kremlin-Bicêtre,
    France

    Active - Recruiting

  • Clinical Trial Site

    Marseille,
    France

    Active - Recruiting

  • Clinical Trial Site

    Berlin,
    Germany

    Active - Recruiting

  • Clinical Trial Site

    Giessen,
    Germany

    Active - Recruiting

  • Clinical Trial Site

    Hanover,
    Germany

    Active - Recruiting

  • Clinical Trial Site

    Jerusalem,
    Israel

    Active - Recruiting

  • Clinical Trial Site

    Ramat Gan,
    Israel

    Active - Recruiting

  • Clinical Trial Site

    Milan,
    Italy

    Active - Recruiting

  • Clinical Trial Site

    Naples,
    Italy

    Active - Recruiting

  • Clinical Trial Site

    Palermo,
    Italy

    Active - Recruiting

  • Clinical Trial Site

    Roma,
    Italy

    Active - Recruiting

  • Clinical Trial Site

    Groningen,
    Netherlands

    Active - Recruiting

  • Clinical Trial Site

    Lisbon,
    Portugal

    Active - Recruiting

  • Clinical Trial Site

    Porto,
    Portugal

    Active - Recruiting

  • Clinical Trial Site

    Barcelona,
    Spain

    Active - Recruiting

  • Clinical Trial Site

    Madrid,
    Spain

    Active - Recruiting

  • Clinical Trial Site

    Palma,
    Spain

    Active - Recruiting

  • Clinical Trial Site

    New Taipei City,
    Taiwan

    Active - Recruiting

  • Clinical Trial Site

    Taipei,
    Taiwan

    Active - Recruiting

  • Clinical Trial Site

    La Jolla, California 92037
    United States

    Active - Recruiting

  • Clinical Trial Site

    Los Angeles, California 90095
    United States

    Active - Recruiting

  • Clinical Trial Site

    Jacksonville, Florida 32224
    United States

    Active - Recruiting

  • Clinical Trial Site

    Iowa City, Iowa 52242
    United States

    Active - Recruiting

  • Clinical Trial Site

    Kansas City, Kansas 66160
    United States

    Active - Recruiting

  • Clinical Trial Site

    Baltimore, Maryland 21224
    United States

    Active - Recruiting

  • Clinical Trial Site

    Boston, Massachusetts 02127
    United States

    Active - Recruiting

  • Clinical Trial Site

    New York, New York 10034
    United States

    Active - Recruiting

  • Clinical Trial Site

    Durham, North Carolina 27710
    United States

    Active - Recruiting

  • Clinical Trial Site

    Columbus, Ohio 43210
    United States

    Active - Recruiting

  • Clinical Trial Site

    Philadelphia, Pennsylvania 19104
    United States

    Active - Recruiting

  • Clinical Trial Site

    Austin, Texas 78756
    United States

    Active - Recruiting

  • Clinical Trial Site

    Houston, Texas 77030
    United States

    Active - Recruiting

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